Clinical Trials for Alexion Pharmaceuticals

Mitigate Immune-Mediated Loss of Therapeutic Response to Asfotase Alfa (STRENSIQ®) for Hypophosphatasia

ALXN2350 in Adult Participants With BAG3-Associated Dilated Cardiomyopathy

Safety and Efficacy of Tarperprumig in Adult Participants With Anti-Neutrophil Cytoplasmic Antibody (ANCA)-Associated Vasculitis

ALXN2420 Versus Placebo in Combination With Somatostatin Analogs in Participants With Acromegaly

Study of ALXN1920 in Adult Participants With Primary Membranous Nephropathy (PMN)

Study of Re-Treatment With ALXN2220 in Patients With ATTR-CM

A Phase 1b/2 Study of CAR T Cell Therapy Targeting CD19 and BCMA in Participants With Relapsed or Refractory AL Amyloidosis.

Study of Danicopan as Add-on Treatment to Ravulizumab or Eculizumab in Pediatric Participants With PNH Who Have Clinically Significant Extravascular Hemolysis

Early Ravulizumab Treatment Of Anti- AChR Antibody-Positive Generalized Myasthenia Gravis

Study of Ravulizumab in Pediatric Participants With Primary IgAN

Double-blind, Randomized, Placebo-controlled, Multicenter Study to Evaluate the Efficacy and Safety of Ravulizumab Administered Intravenously in Adult Participants at High Risk of Delayed Graft Function After Kidney Transplantation

Phase 2 Study of ALXN2030 in Patients With Antibody-Mediated Rejection After Kidney Transplantation

Efficacy, Safety, PK, PD, and ADA of Eculizumab in Chinese Adults With NMOSD

Efficacy, Safety, Pharmacokinetics, Pharmacodynamics, and Immunogenicity of Eculizumab in Chinese Adults With gMG

Study of Ultomiris® (Ravulizumab) Safety in Pregnancy

PK, PD, Safety, and Efficacy Study of Gefurulimab in Pediatric Patients With AChR+ Generalized Myasthenia Gravis

Acceptability and Safety of MR-C-014 in Persons With Neuromyelitis Optica Spectrum Disorder

Efficacy, Safety, Pharmacokinetics, Pharmacodynamics, and Immunogenicity of Ravulizumab in Chinese Adults Participants With Paroxysmal Nocturnal Hemoglobinuria (PNH)

Study of the Clinical and Radiological Impact of Ravulizumab in People With Neuromyelitis Optica Spectrum Disorder

Phase 3 Study of ALXN1850 in Treatment-Naïve Pediatric Participants With HPP

Phase 3 Study of ALXN1850 in Pediatric Participants With HPP Previously Treated With Asfotase Alfa

Study of Ravulizumab in Immunoglobulin A Nephropathy (IgAN)

Registry of Patients With AQP4+ NMOSD Treated With Alexion C5 Inhibitor Therapies

Study of ALXN2220 Versus Placebo in Adults With ATTR-CM

Phase 3 Study of ALXN1850 Versus Placebo in Adolescent and Adult Participants With HPP Who Have Not Previously Been Treated With Asfotase Alfa

Evaluation of Pharmacokinetics, Pharmacodynamics, Efficacy, Safety, and Immunogenicity of Ravulizumab Administered Intravenously in Pediatric Participants With Generalized Myasthenia Gravis (gMG)

Evaluation of the Safety and Efficacy of Eneboparatide (AZP-3601) in Patients With Chronic Hypoparathyroidism

ARTEMIS: Ravulizumab to Protect Patients With CKD From CSA-AKI and MAKE

Safety and Efficacy of ALXN1720 in Adults With Generalized Myasthenia Gravis

A Long-term Safety and Efficacy Study of Danicopan as an Add-on Therapy to Complement Component 5 Inhibitor (C5i) in Participants With PNH

A Study About the Natural History in Adults With BAG3 Dilated Cardiomyopathy (a Type of Heart Disease) (BAG3 DCM)

A Prospective Sub-Study of the Global Hypophosphatasia Registry

Safety, PK/PD, and Immunogenicity Study of SC ALXN2030 in Healthy Participants

Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy

Efficacy and Safety Study of Ravulizumab IV in Pediatric Participants With NMOSD

ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program

Ravulizumab in Thrombotic Microangiopathy After Hematopoietic Stem Cell Transplant

A Phase 3 Study of ALXN2060 in Japanese Participants With Symptomatic ATTR-CM

A Study to Evaluate the Efficacy and Safety of CAEL-101 in Patients With Mayo Stage IIIa AL Amyloidosis (CARES)

A Study to Evaluate the Efficacy and Safety of CAEL-101 in Patients With Mayo Stage IIIb AL Amyloidosis (CARES)

Registry of Participants With Generalized Myasthenia Gravis Treated With Alexion C5 Inhibition Therapies (C5ITs)

Paroxysmal Nocturnal Hemoglobinuria in ESUS & ETUS

Registry of Patients With Hypophosphatasia

Lysosomal Acid Lipase (LAL) Deficiency Registry

Atypical Hemolytic-Uremic Syndrome (aHUS) Registry