18
Participants
Start Date
December 31, 2025
Primary Completion Date
July 31, 2030
Study Completion Date
April 1, 2032
ALXN2350
ALXN2350 is a gene therapy product consisting of an AAV9 capsid containing BAG3 transgene. It is administered as a single intravenous (IV) infusion.
Lead Sponsor
Alexion Pharmaceuticals, Inc.
INDUSTRY