ALXN2350 in Adult Participants With BAG3-Associated Dilated Cardiomyopathy

PHASE1/PHASE2Not yet recruitingINTERVENTIONAL
Enrollment

18

Participants

Timeline

Start Date

December 31, 2025

Primary Completion Date

July 31, 2030

Study Completion Date

April 1, 2032

Conditions
BAG3 Mutation Associated Dilated Cardiomyopathy
Interventions
DRUG

ALXN2350

ALXN2350 is a gene therapy product consisting of an AAV9 capsid containing BAG3 transgene. It is administered as a single intravenous (IV) infusion.

Sponsors
All Listed Sponsors
lead

Alexion Pharmaceuticals, Inc.

INDUSTRY