A Prospective Sub-Study of the Global Hypophosphatasia Registry

RecruitingOBSERVATIONAL
Enrollment

30

Participants

Timeline

Start Date

August 25, 2022

Primary Completion Date

July 18, 2028

Study Completion Date

July 18, 2028

Conditions
Hypophosphatasia
Interventions
BIOLOGICAL

Asfotase Alfa

All participants will receive asfotase alfa subcutaneously per standard of care. Unless otherwise specified per the Physician's standard of care, participants aged \< 2 years are recommended for a clinic visit approximately every 3 months after Enrollment until 2 years of age, after which they should have a clinic visit approximately every 6 months. Participants should be followed for 5 years, as possible.

Trial Locations (12)

11501

RECRUITING

Clinical Trial Site, Mineola

15224

NOT_YET_RECRUITING

Clinical Trial Site, Pittsburgh

22903

RECRUITING

Clinical Trial Site, Charlottesville

37112

RECRUITING

Clinical Trial Site, Nashville

43203

RECRUITING

Clinical Trial Site, Columbus

45229

NOT_YET_RECRUITING

Clinical Trial Site, Cincinnati

53792

RECRUITING

Clinical Trial Site, Madison

60611

RECRUITING

Clinical Trial Site, Chicago

64108

RECRUITING

Clinical Trial Site, Kansas City

84108

RECRUITING

Clinical Trial Site, Salt Lake City

06106

RECRUITING

Clinical Trial Site, Hartford

02122

RECRUITING

Clinical Trial Site, Boston

Sponsors
All Listed Sponsors
lead

Alexion Pharmaceuticals, Inc.

INDUSTRY