Efficacy and Safety Study of Ravulizumab IV in Pediatric Participants With NMOSD

PHASE2/PHASE3RecruitingINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

June 23, 2022

Primary Completion Date

March 31, 2026

Study Completion Date

January 2, 2029

Conditions
Neuromyelitis Optica Spectrum Disorder
Interventions
DRUG

Ravulizumab

"Participants will receive a weight-based loading dose of ravulizumab on Day 1, followed by weight-based maintenance treatment with ravulizumab on Day 15 and every 8 weeks (q8w) after or once every 4 weeks (q4w) depending on weight.~During the Extension Period, participants will continue to receive weight-based maintenance doses of ravulizumab IV on Day 351 and q8w or q4w, depending on weight."

Trial Locations (21)

8950

RECRUITING

Research Site, Esplugues de Llobregat

10408

RECRUITING

Research Site, Goyang-si

13005

RECRUITING

Research Site, Marseille

19104

RECRUITING

Research Site, Philadelphia

20010

RECRUITING

Research Site, Washington D.C.

21013

RECRUITING

Research Site, Gallarate

27705

RECRUITING

Research Site, Durham

33136

RECRUITING

Research Site, Miami

34295

RECRUITING

Research Site, Montpellier

35392

WITHDRAWN

Research Site, Giessen

44791

WITHDRAWN

Research Site, Bochum

63110

WITHDRAWN

Research Site, St Louis

66013

RECRUITING

Research Site, Chieti

94270

RECRUITING

Research Site, Le Kremlin-Bicêtre

95123

WITHDRAWN

Research Site, Catania

02114

RECRUITING

Research Site, Boston

T6G 1C9

RECRUITING

Research Site, Edmonton

M5G 1X8

RECRUITING

Research Site, Toronto

H3T1C5

RECRUITING

Research Site, Montreal

00165

RECRUITING

Research Site, Roma

232-0024

RECRUITING

Research Site, Yokohama

Sponsors
All Listed Sponsors
lead

Alexion Pharmaceuticals, Inc.

INDUSTRY