NCT05506254View on ClinicalTrials.gov

Long-term Follow-up Study of Patients Who Received hLB-001 Gene Therapy

Active, not recruitingOBSERVATIONAL
Enrollment

4

Participants

Timeline

Start Date

July 15, 2022

Primary Completion Date

January 1, 2037

Study Completion Date

January 1, 2037

Conditions
Methylmalonic Acidemia
Interventions
DRUG

hLB-001

hLB-001 gene therapy

Trial Locations (4)

15224

Clinical Trial Site, Pittsburgh

30322

Clinical Trial Site, Atlanta

37232

Clinical Trial Site, Nashville

98105

Clinical Trial Site, Seattle

Sponsors
All Listed Sponsors
lead

Alexion Pharmaceuticals, Inc.

INDUSTRY