Lysosomal Acid Lipase (LAL) Deficiency Registry

RecruitingOBSERVATIONAL
Enrollment

300

Participants

Timeline

Start Date

May 30, 2013

Primary Completion Date

August 30, 2029

Study Completion Date

August 30, 2029

Conditions
Lysosomal Acid Lipase DeficiencyCholesterol Ester Storage DiseaseWolman DiseaseAcid Cholesteryl Ester Hydrolase Deficiency, Type 2Acid Lipase DeficiencyLIPA DeficiencyLAL-Deficiency
Trial Locations (104)

1105

RECRUITING

Clinical Trial Site, Amsterdam

RECRUITING

Clinical Trial Site, Amsterdam

1111

RECRUITING

Clinical Trial Site, Ljubljana

1612

RECRUITING

Clinical Trial Site, Sofia

1649

RECRUITING

Clinical Trial Site, Lisbon

2305

RECRUITING

Clinical Trial Site, New Lambton Heights

4835

RECRUITING

Clinical Trial Site, Guimarães

9000

RECRUITING

Clinical Trial Site, Ghent

10000

RECRUITING

Clinical Trial Site, Zagreb

10016

RECRUITING

Clinical Trial Site, New York

10126

RECRUITING

Clinical Trial Site, Turin

10467

RECRUITING

Clinical Trial Site, The Bronx

11211

RECRUITING

Clinical Trial Site, Riyadh

11426

RECRUITING

Clinical Trial Site, Riyadh

13353

RECRUITING

Clinical Trial Site, Berlin

14033

RECRUITING

Clinical Trial Site, Caen

15006

RECRUITING

Clinical Trial Site, A Coruña

15706

RECRUITING

Clinical Trial Site, Santiago de Compostela

16147

RECRUITING

Clinical Trial Site, Genoa

17000

RECRUITING

Clinical Trial Site, La Rochelle

19104

RECRUITING

Clinical Trial Site, Philadelphia

19107

RECRUITING

Clinical Trial Site, Philadelphia

20122

RECRUITING

Clinical Trial Site, Milan

20230

RECRUITING

Clinical Trial Site, Aguascalientes

21000

RECRUITING

Clinical Trial Site, Dijon

24127

RECRUITING

Clinical Trial Site, Bergamo

26006

RECRUITING

Clinical Trial Site, Logroño

27880

RECRUITING

Clinical Trial Site, Burela de Cabo

28046

RECRUITING

Clinical Trial Site, Madrid

28914

RECRUITING

Clinical Trial Site, Madrid

29010

RECRUITING

Clinical Trial Site, Málaga

30120

RECRUITING

Clinical Trial Site, Murcia

30322

RECRUITING

Clinical Trial Site, Atlanta

32806

RECRUITING

Clinical Trial Site, Orlando

33011

RECRUITING

Clinical Trial Site, Oviedo

33025

RECRUITING

Clinical Trial Site, Miramar

33100

RECRUITING

Clinical Trial Site, Udine

35019

RECRUITING

Clinical Trial Site, Las Palmas

35128

RECRUITING

Clinical Trial Site, Padua

38043

RECRUITING

Clinical Trial Site, Grenoble

39216

RECRUITING

Clinical Trial Site, Jackson

43204

RECRUITING

Clinical Trial Site, Reus

44093

RECRUITING

Clinical Trial Site, Nantes

45116

RECRUITING

Clinical Trial Site, Zapopan

45122

RECRUITING

Clinical Trial Site, Essen

47012

RECRUITING

Clinical Trial Site, Valladolid

48236

RECRUITING

Clinical Trial Site, Detroit

48903

RECRUITING

Clinical Trial Site, Barakaldo

49202

RECRUITING

Clinical Trial Site, Petah Tikva

50009

RECRUITING

Clinical Trial Site, Zaragoza

50139

RECRUITING

Clinical Trial Site, Florence

54500

RECRUITING

Clinical Trial Site, Nancy

55131

RECRUITING

Clinical Trial Site, Mainz

55404

RECRUITING

Clinical Trial Site, Minneapolis

60611

RECRUITING

Clinical Trial Site, Chicago

63003

RECRUITING

Clinical Trial Site, Clermont-Ferrand

63100

RECRUITING

Clinical Trial Site, Clermont-Ferrand

69500

RECRUITING

Clinical Trial Site, Bron

70126

RECRUITING

Clinical Trial Site, Bari

75743

RECRUITING

Clinical Trial Site, Paris

77030

RECRUITING

Clinical Trial Site, Houston

RECRUITING

Clinical Trial Site, Houston

79021

RECRUITING

Clinical Trial Site, Niort

79549

RECRUITING

Clinical Trial Site, Snyder

80131

RECRUITING

Clinical Trial Site, Napoli

81377

RECRUITING

Clinical Trial Site, Munich

85016

RECRUITING

Clinical Trial Site, Phoenix

91120

RECRUITING

Clinical Trial Site, Jerusalem

94305

RECRUITING

Clinical Trial Site, Stanford

98405

RECRUITING

Clinical Trial Site, Tacoma

115446

RECRUITING

Clinical Trial Site, Moscow

119049

RECRUITING

Clinical Trial Site, Moscow

119192

RECRUITING

Clinical Trial Site, Moscow

119296

RECRUITING

Clinical Trial Site, Moscow

194100

RECRUITING

Clinical Trial Site, Petersburg

603950

RECRUITING

Clinical Trial Site, Nizhny Novgorod

3436212

RECRUITING

Clinical Trial Site, Haifa

9103102

RECRUITING

Clinical Trial Site, Jerusalem

02115

RECRUITING

Clinical Trial Site, Boston

07601

RECRUITING

Clinical Trial Site, Hackensack, NJ, 7601

19104-6061

RECRUITING

Clinical Trial Site, Philadelphia

13083-878

RECRUITING

Clinical Trial Site, Campinas

04020-041

RECRUITING

Clinical Trial Site, São Paulo

04543-011

RECRUITING

Clinical Trial Site, São Paulo

T6G 2H7

RECRUITING

Clinical Trial Site, Edmonton

B3H 1V8

RECRUITING

Clinical Trial Site, Halifax

NGA 5W9

RECRUITING

Clinical Trial Site, London

G1R 2J6

RECRUITING

Clinical Trial Site, Québec

128 00

RECRUITING

Clinical Trial Site, Prague

779 00

RECRUITING

Clinical Trial Site, Olomouc

115 27

RECRUITING

Clinical Trial Site, Athens

455 00

RECRUITING

Clinical Trial Site, Ioannina

564 03

RECRUITING

Clinical Trial Site, Thessaloniki

D01 XD99

RECRUITING

Clinical Trial Site, Dublin

06720

RECRUITING

Clinical Trial Site, Mexico City

02006

RECRUITING

Clinical Trial Site, Albacete

03203

RECRUITING

Clinical Trial Site, Alicante

08036

RECRUITING

Clinical Trial Site, Barcelona

08305

RECRUITING

Clinical Trial Site, Barcelona

CB2 0QQ

RECRUITING

Clinical Trial Site, Cambridge

WC1N 3BG

RECRUITING

Clinical Trial Site, London

M13 9WL

RECRUITING

Clinical Trial Site, Manchester

M6 8HD

RECRUITING

Clinical Trial Site, Salford

B4 6NH

RECRUITING

Clinical Trial Site, Birmingham

Sponsors
All Listed Sponsors
lead

Alexion Pharmaceuticals, Inc.

INDUSTRY