A Long-term Safety and Efficacy Study of Danicopan as an Add-on Therapy to Complement Component 5 Inhibitor (C5i) in Participants With PNH

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

80

Participants

Timeline

Start Date

October 28, 2022

Primary Completion Date

July 31, 2026

Study Completion Date

July 31, 2026

Conditions
Paroxysmal Nocturnal Hemoglobinuria
Interventions
DRUG

Danicopan

Oral tablet

Trial Locations (45)

161

Research Site, Roma

8916

Research Site, Badalona

10330

Research Site, Bangkok

11101

Research Site, Long Island City

11527

Research Site, Athens

16247

Research Site, Suwon

20122

Research Site, Milan

21231

Research Site, Baltimore

28222

Research Site, Majadahonda

31048

Research Site, Haifa

33604

Research Site, Pessac

36061

Research Site, Bassano del Grappa

41013

Research Site, Seville

44195

Research Site, Cleveland

50134

Research Site, Florence

57010

Research Site, Thessaloniki

59037

Research Site, Lille

60612

Research Site, Chicago

64111

Research Site, Kansas City

69495

Research Site, Pierre-Bénite

75010

Research Site, Paris

83100

Research Site, Avellino

88586

Research Site, Kota Kinabalu

89131

Research Site, Reggio Calabria

90089

Research Site, Los Angeles

91120

Research Site, Jerusalem

93200

Research Site, Kuching

98000

Research Site, Miri

75390-9047

Research Site, Dallas

90110-270

Research Site, Porto Alegre

20211-080

Research Site, Rio de Janeiro

M5G 2C4

Research Site, Toronto

625 00

Research Site, Brno

113 8603

Research Site, Bunkyō City

605-0981

Research Site, Kyoto

530-8480

Research Site, Osaka

150-8935

Research Site, Shibuya-ku

305-8576

Research Site, Tsukuba

80-952

Research Site, Gdansk

03722

Research Site, Seoul

06591

Research Site, Seoul

08036

Research Site, Barcelona

ML6 0JS

Research Site, Airdrie

LS9 7TF

Research Site, Leeds

SE5 9RS

Research Site, London

Sponsors
All Listed Sponsors
lead

Alexion Pharmaceuticals, Inc.

INDUSTRY