Cell Therapies focused on CAR T, oncology
Total Trials
10
As Lead Sponsor
8
As Collaborator
2
Total Enrollment
931
NCT04064307
Myotubular and Centronuclear Myopathy Patient Registry
Phase: N/A
Role: Collaborator
Start: Mar 26, 2013
Completion: May 31, 2025
NCT02231697
A Medical Chart Review of Patients With X-Linked Myotubular Myopathy (XLMTM)
Role: Lead Sponsor
Start: Sep 30, 2014
Completion: Dec 31, 2019
NCT02704273
A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects
Start: Jul 31, 2016
Completion: Sep 30, 2019
NCT03199469
A Study of AT132 in Young Children With X-Linked Myotubular Myopathy (XLMTM)
Phase: Phase 2/3
Start: Aug 2, 2017
Completion: Mar 31, 2030
NCT04174105
Gene Transfer Study in Patients With Late Onset Pompe Disease
Phase: Phase 1/2
Start: Oct 27, 2020
Completion: Feb 28, 2030
NCT06150820
A Study About Antibody Levels and Biomarkers in the Blood in People With Late-onset Pompe Disease
Start: Feb 1, 2024
Completion: Jun 30, 2027
NCT06422208
Autologous iPSC-Derived Dopamine Neuron Transplantation for Parkinson's Disease
Phase: Phase 1
Start: Aug 7, 2024
Completion: Dec 31, 2027
NCT06483802
A Study of ASP2016 in Adults Who Have Heart Disease Associated With Friedreich Ataxia
Start: Nov 8, 2024
Completion: Jan 31, 2031
NCT06581146
A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition
Start: May 19, 2025
Completion: May 31, 2027
NCT07052929
Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators
Start: Sep 11, 2025
Completion: Oct 31, 2027
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