NCT07052929View on ClinicalTrials.gov

Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators

PHASE1/PHASE2RecruitingINTERVENTIONAL
Enrollment

9

Participants

Timeline

Start Date

September 11, 2025

Primary Completion Date

October 31, 2027

Study Completion Date

October 31, 2027

Conditions
X-Linked Myotubular Myopathy
Interventions
GENETIC

ASP2957

Intravenous infusion

DRUG

Methylprednisolone

Intravenous infusion

DRUG

Prednisolone

Route of administration based on locally sourced product

DRUG

Sirolimus

Route of administration based on locally sourced product

Trial Locations (1)

60611

RECRUITING

Lurie Children's Hospital, Chicago

Sponsors
All Listed Sponsors
lead

Astellas Gene Therapies

INDUSTRY