161
Participants
Start Date
September 30, 2014
Primary Completion Date
December 31, 2019
Study Completion Date
December 31, 2019
Non-interventional, retrospective medical chart review
Non-interventional, retrospective medical chart review
The Children's Hospital of Philadelphia, Philadelphia
University of Florida - Gainesville, Children's Research Institute, Gainesville
Lurie Children's Hospital, Chicago
Children's Hospital Colorado, Aurora
Cure CMD, San Pedro
Boston Children's Hospital, Boston
Great Ormond Street Hospital, London
Royal Manchester Children's Hospital, Manchester
Lead Sponsor
Astellas Gene Therapies
INDUSTRY