A Medical Chart Review of Patients With X-Linked Myotubular Myopathy (XLMTM)

CompletedOBSERVATIONAL
Enrollment

161

Participants

Timeline

Start Date

September 30, 2014

Primary Completion Date

December 31, 2019

Study Completion Date

December 31, 2019

Conditions
Males With X-linked Myotubular Myopathy (XLMTM)
Interventions
OTHER

Non-interventional, retrospective medical chart review

Non-interventional, retrospective medical chart review

Trial Locations (8)

19104

The Children's Hospital of Philadelphia, Philadelphia

32610

University of Florida - Gainesville, Children's Research Institute, Gainesville

60611

Lurie Children's Hospital, Chicago

80045

Children's Hospital Colorado, Aurora

90732

Cure CMD, San Pedro

02115

Boston Children's Hospital, Boston

Unknown

Great Ormond Street Hospital, London

Royal Manchester Children's Hospital, Manchester

Sponsors
All Listed Sponsors
lead

Astellas Gene Therapies

INDUSTRY

NCT02231697 - A Medical Chart Review of Patients With X-Linked Myotubular Myopathy (XLMTM) | Biotech Hunter | Biotech Hunter