A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects

CompletedOBSERVATIONAL
Enrollment

34

Participants

Timeline

Start Date

July 31, 2016

Primary Completion Date

September 30, 2019

Study Completion Date

September 30, 2019

Conditions
X-linked Myotubular Myopathy
Trial Locations (8)

20892

National Institute of Neurological Disorders and Stroke/NIH Porter, Bethesda

32610

University of Florida, Gainesville

60611

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago

75012

Hopital Armand Trousseau, Paris

90095

UCLA, Los Angeles

803337

Ludwig-Maximilians Universität München, Munich

M5G0A4

Hospital for Sick Children, Toronto

Unknown

Great Ormond Street Hospital, London

Sponsors
All Listed Sponsors
lead

Astellas Gene Therapies

INDUSTRY

NCT02704273 - A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects | Biotech Hunter | Biotech Hunter