34
Participants
Start Date
July 31, 2016
Primary Completion Date
September 30, 2019
Study Completion Date
September 30, 2019
National Institute of Neurological Disorders and Stroke/NIH Porter, Bethesda
University of Florida, Gainesville
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Hopital Armand Trousseau, Paris
UCLA, Los Angeles
Ludwig-Maximilians Universität München, Munich
Hospital for Sick Children, Toronto
Great Ormond Street Hospital, London
Lead Sponsor
Astellas Gene Therapies
INDUSTRY