A Study of ASP2016 in Adults Who Have Heart Disease Associated With Friedreich Ataxia

PHASE1SuspendedINTERVENTIONAL
Enrollment

14

Participants

Timeline

Start Date

November 8, 2024

Primary Completion Date

January 31, 2031

Study Completion Date

January 31, 2031

Conditions
Friedreich AtaxiaCardiomyopathy
Interventions
GENETIC

ASP2016

Intravenous (IV) infusion

DRUG

Prednisolone

Oral

Trial Locations (5)

32608

University of Florida, Gainesville

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

77030

University of Texas - Houston, Houston

90095

University of California - Los Angeles, Los Angeles

02115

Boston Children's Hospital, Boston

Sponsors
All Listed Sponsors
lead

Astellas Gene Therapies

INDUSTRY