14
Participants
Start Date
November 8, 2024
Primary Completion Date
January 31, 2031
Study Completion Date
January 31, 2031
ASP2016
Intravenous (IV) infusion
Prednisolone
Oral
University of Florida, Gainesville
Cincinnati Children's Hospital Medical Center, Cincinnati
University of Texas - Houston, Houston
University of California - Los Angeles, Los Angeles
Boston Children's Hospital, Boston
Lead Sponsor
Astellas Gene Therapies
INDUSTRY