27
Participants
Start Date
August 2, 2017
Primary Completion Date
September 9, 2021
Study Completion Date
March 31, 2030
Resamirigene bilparvovec
Resamirigene bilparvovec is an AAV8 vector containing a functional copy of the human MTM1 (hMTM1) gene.
Ann & Robert H Lurie Children's Hospital of Chicago, Chicago
Hopital Armad Trousseau, Paris
Kinderklinik und Kinderpoliklinik im Dr. Von Haunerschen Kinderspital Klinikum der Universitat Munchen, München
UCLA Medical Center, Los Angeles
National Institute of Neurological Disorders and Stroke/NIH Porter, Bethesda
Hospital for Sick Children, Toronto
Lead Sponsor
Astellas Gene Therapies
INDUSTRY