NCT06581146View on ClinicalTrials.gov

A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition

RecruitingOBSERVATIONAL
Enrollment

50

Participants

Timeline

Start Date

May 19, 2025

Primary Completion Date

May 31, 2027

Study Completion Date

May 31, 2027

Conditions
X-Linked Myotubular Myopathy
Interventions
OTHER

No Intervention

No investigational drug will be administered to participants in this study.

Trial Locations (3)

19104

RECRUITING

Children's Hospital of Philadelphia, Philadelphia

60611

RECRUITING

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago

02115

RECRUITING

Boston Children's Hospital, Boston

Sponsors
All Listed Sponsors
lead

Astellas Gene Therapies

INDUSTRY

NCT06581146 - A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition | Biotech Hunter | Biotech Hunter