Clinical Trials for PTC Therapeutics

Explore 9 clinical trials worldwide

Showing 1-9 of 9 trials

Active filters:Status: Recruiting, Active, not recruiting, Enrolling by invitation, Not yet recruitingSponsor: PTC Therapeutics

Clinical Trials (9)

NCT06302348
A Study of Sepiapterin in Participants With Phenylketonuria (PKU)
PHASE3Recruiting
56 participants
Started: Mar 4, 2024 · Completed: Feb 28, 2031
1 condition1 sponsor1 location
NCT06254482
An Extension Study to Evaluate the Long-Term Safety and Efficacy of PTC518 in Participants With Huntington's Disease (HD)
PHASE2Enrolling by invitation
250 participants
Started: Aug 25, 2023 · Completed: Jul 20, 2027
1 condition1 sponsor24 locations
NCT05515536
A Study to Assess the Safety and Efficacy of Vatiquinone in Participants With Friedreich Ataxia
PHASE3Active, not recruiting
130 participants
Started: Dec 8, 2022 · Completed: Dec 31, 2027
1 condition1 sponsor14 locations
NCT05358717
A Study to Evaluate the Safety and Efficacy of PTC518 in Participants With Huntington's Disease (HD)
PHASE2Active, not recruiting
252 participants
Started: Apr 25, 2022 · Completed: Aug 15, 2025
1 condition1 sponsor28 locations
NCT05166161
A Long-Term Safety Study of PTC923 in Participants With Phenylketonuria
PHASE3Recruiting
200 participants
Started: Feb 14, 2022 · Completed: Apr 30, 2026
1 condition1 sponsor45 locations
NCT04903288
A Study of SmartFlow Magnetic Resonance (MR) Compatible Ventricular Cannula for Administering Eladocagene Exuparvovec to Pediatric Participants
PHASE2Active, not recruiting
13 participants
Started: May 12, 2021 · Completed: Apr 30, 2028
1 condition1 sponsor6 locations
NCT03605550
A Phase 1b Study of PTC596 in Children With Newly Diagnosed Diffuse Intrinsic Pontine Glioma and High Grade Glioma
PHASE1Active, not recruiting
64 participants
Started: Aug 1, 2018 · Completed: Mar 1, 2029
2 conditions2 sponsors10 locations
NCT02369731
Registry of Translarna (Ataluren) in Nonsense Mutation Duchenne Muscular Dystrophy (nmDMD)
N/AActive, not recruiting
316 participants
Started: Apr 30, 2015 · Completed: May 30, 2025
1 condition3 sponsors71 locations
NCT01247207
Study of Ataluren in Previously Treated Participants With Nonsense Mutation Dystrophinopathy (nmDBMD)
PHASE3Enrolling by invitation
270 participants
Started: Nov 30, 2010 · Completed: Apr 30, 2025
1 condition1 sponsor34 locations