200
Participants
Start Date
February 14, 2022
Primary Completion Date
April 30, 2026
Study Completion Date
April 30, 2026
PTC923
PTC923 powder for oral use will be suspended in water or apple juice prior to administration.
RECRUITING
Univerzitetni klinicni center Ljubljana, Ljubljana
RECRUITING
Westmead Hospital, Westmead
RECRUITING
Royal Children's Hospital, Parkville
RECRUITING
Icahn School of Medicine at Mount Sinai (ISMMS), New York
RECRUITING
UPMC Children's Hospital of Pittsburgh, Pittsburgh
RECRUITING
University Children's Hospital Hamburg Eppendorf (Kinder-UKE) Klinik für Kinder- und Jugendmedizin (Kinder-UKE), Hamburg
RECRUITING
Hospital Universitario Ramón y Cajal, Madrid
RECRUITING
UF College of Medicine, Department of Pediatrics Division of Genetics and Metabolism, Gainesville
RECRUITING
İstanbul Üniversitesi Cerrahpaşa Tıp Fakültesi, Fatih
RECRUITING
Ege University Faculty of Medicine Children Hospital, Bornova
RECRUITING
Azienda Ospedaliera-Universita Padova, Padua
RECRUITING
Hospital Universitario Virgen del Rocío, Seville
RECRUITING
PanAmerican Clinical Research, Guadalajara
RECRUITING
Indiana University School of Medicine Department of Medical and Molecular Genetics, Indianapolis
RECRUITING
Universitätsklinikum Münster, Münster
RECRUITING
Universitätsklinikum Heidelberg / Zentrum für Kinder- und Jugendmedizin / Sektion für Neuropädiatrie & Stoffwechselmedizin, Heidelberg
RECRUITING
Hôpital Necker-Enfants Malades - Centre de Référence des Maladies Héréditaires du Métabolisme, Paris
RECRUITING
Children's Hospital Colorado, Aurora
RECRUITING
University of Utah, Salt Lake City
ACTIVE_NOT_RECRUITING
Boston Children's Hospital, Boston
RECRUITING
PARC Clinical Research, Adelaide
RECRUITING
Hospital de clinicas de Porto Alegre, Porto Alegre
RECRUITING
Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto da Universidade de São Paulo, Ribeirão Preto
RECRUITING
Metabolics and Genetics in Calgary (MAGIC) Clinic, Ltd., Calgary
RECRUITING
McMaster Children's Hospital Hamilton Health Sciences, Hamilton
RECRUITING
The Hospital for Sick Children University of Toronto Adult Clinic: The Fred A Litwin Family Centre in Genetic Medicine University Health Network & Mt. Sinai Hospital, Toronto
RECRUITING
Fakultní nemocnice Královské Vinohrady Klinika dětí a dorostu Ambulance pro léčbu PKU a HPA, Prague
RECRUITING
Copenhagen University Hospital, Rigshospitalet, Copenhagen
RECRUITING
Medical Genetics and Laboratory Diagnostics Center, Tbilisi
RECRUITING
Department of Human Neuroscience, Child and Adolescent Neuropsychiatry, Policlinico Umberto I, Rome
RECRUITING
PTC Clinical Site 1, Multiple Locations
RECRUITING
PTC Clinical Site 2, Multiple Locations
RECRUITING
PTC Clinical Site 3, Multiple Locations
RECRUITING
UNIVERSITY HOSPITALS BIRMINGHAM NHS Foundation Trust, Birmingham
RECRUITING
UMCG Beatrix Children's Hospital, Groningen
RECRUITING
Pomorski Uniwersytet Medyczny w Szczecinie Centrum Wsparcia Badań Klinicznych, Szczecin
RECRUITING
CENTRO HOSPITALAR UNIVERSITÁRIO LISBOA NORTE Hospital de Santa Maria,, Lisbon
RECRUITING
CENTRO HOSPITALAR UNIVERSITÁRIO LISBOA NORTE Hospital de Santa Maria, Lisbon
RECRUITING
Centro Hospitalar Universitário Do Porto, Epe, Porto
RECRUITING
Hospital Sant Joan de Déu, Barcelona
RECRUITING
Hacettepe University Medical Faculty, Altındağ
RECRUITING
Gazi Üniversitesi Tıp Fakültesi, Yenimahalle
RECRUITING
Çukurova Üniversitesi Tıp Fakültesi Balcalı Hastanesi, Adana
RECRUITING
Birmingham Children's Hospital NHS Foundation Trust, Birmingham
RECRUITING
Great Ormond Street Hospital, London
Lead Sponsor
PTC Therapeutics
INDUSTRY