316
Participants
Start Date
April 30, 2015
Primary Completion Date
May 30, 2025
Study Completion Date
May 30, 2025
University Children's Hospital University Medical Centre Ljubljana, Ljubljana
Sozialmedizinisches Zentrum Süd Kaiser-Franz-Josef Spital mit Gottfried von Preyer´schen Kinderspital, Vienna
Krankenhaus der Barmherzigen Schwestern Linz, Linz
Ospedale Molinette SCDU Neuropsichiatria Infantile AO Città della Salute e della Scienza di Torino, Torino
"Children's Hospital Aghia Sophia", Athens
Sozialpädiatrisches Zentrum (SPZ) Charité Berlin, Berlin
CHU de Marseille Hôpital de la Timone, Marseille
Motol University Hospital, Praha 5 - Motol
Istituto Giannina Gaslini, Genova
Karolinska Institutet, Stockholm
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan
IRCCS Istituto Neurologico Carlo Besta, Milan
ASST Grande Ospedale Metropolitano Niguarda, Milan
Klinik und Poliklinik f. Kinder- und Jugendmedizin, Hamburg
"Spitalul Clinic de Copii Dr. Victor Gomoiu Sectia Clinica Neurologie Pediatrica", Bucharest
CHRU de Brest Hôpital Morvan, Brest
CHU de Toulouse Hôpital Pierre Paul Riquet, Toulouse
CHU de Bordeaux Hôpital Pellegrin Enfant, Bordeaux
Muskelzentrum, Schwerpunkt Neuropädiatrie, Kassel
AO Padova Clinica Neurologica, Padua
Universitätskinderklinik Gießen, Giessen
CHRU de Tours Hôpital Bretonneau, Tours
IRCSS Istituto delle Scienze Neurologiche, Bologna
Göteborgs Universitet Avdelningen för pediatrik vid institutionen för kliniska vetenskaper, Gothenburg
CHU de Saint-Etienne Hôpital Bellevue, Saint-Etienne
CHU de Nantes, Nantes
Universitaetsklinikum Essen (AoR), Essen
Schneider Medical Center Tel Aviv University, Petah Tikva
CHU de Reims American Memorial Hospital, Reims
Sheba Medical Center The Joseph Sagol EMG, Neuroscience Center, Ramat Gan
CHU de Nancy Hôpital de Brabois-Enfants Rue du Morvan, Vandœuvre-lès-Nancy
Ahepa University Hospital, Thessaloniki
CHRU de Lille, Lille
SPZ Frankfurt Mitte, Frankfurt am Main
The University Hospital Brno, Brno
CHU de Clermont-Ferrand, hôpital Estaing, Clermont-Ferrand
CHU de Strasbourg, Strasbourg
"Hospices Civils de Lyon Groupement Hospitalier Est - Bâtiment Les Tilleuls", Bron
Hôpital Armand Trousseau, Paris
Hôpital Necker - Enfants malades, Paris
Universitaetsklinikum Freiburg, Freiburg im Breisgau
II Policlinico Neurofisiopatologia (Edificio 11 G), Napoli
Cardiomiologia e Genetica Medica Primo Policlinico, Napoli
MVZ Kinder- und Jugendärzte Fürth GmbH, Fürth
Universitätsklinikum Erlangen, Erlangen
Hadassah Mount Scopus Medical Center, Jerusalem
Klinikum Bayreuth GmbH, Bayreuth
CHU de Martinique - Hôpital P. Zobda-Quitman, Fort de France Cedex
CHU de la Réunion - GHSR - GH Sud-Réunion, Saint-Pierre
"AOU Policlinico G. Martino", Messina
Hospital das Clínicas da Universidade de São Paulo, São Paulo
Semmelweis Egyetem II (Semmelweis University II), Budapest
Szent László Kórház Gyermekneurológiai szakrendelés, Budapest
Bērnu klīniskā universitātes slimnīca, Riga
Regina Maria Policlinica Opera Center, Bucharest
Fondazione Policlinico Universitario Agostino Gemelli, Roma
Bambino Gesù Children's Hospital, Rome
St. Olavs hospital University children's clinical hospital, Trondheim
Centro Hospitalar e Universitário de coimbra EPE - Hospital Pediátrico de Coimbra, Coimbra
Centro Hospitalar Lisboa Norte EPE - Hospital de Santa Maria, Lisbon
Centro Hospitalar do Porto EPE - Hospital Geral de Santo António, Porto
Birmingham Heartlands Hospital, Birmingham
Bristol Children's Hospital, Bristol
Addenbrooke's Hospital, Cambridge
Children Hospital - Children's Neurosciences Leeds TEACHING HOSPITALS NHS Trust, Leeds
Children's Hospital Alder Hey Children's Hospital NHS Trust, Liverpool
St Thomas' Hospital Children Services, London
UCL Great Ormond Street Institute of Child Health, London
Royal Manchester Children's Hospital, Manchester
The John Walton Muscular Dystrophy Research Centre, Newcastle
NIHR Lancashire Clinical Research Facility Royal Preston Hospital, Preston
Lead Sponsor
The John Walton Muscular Dystrophy Research Centre (TREAT-NMD)
UNKNOWN
Cooperative International Neuromuscular Research Group
NETWORK
PTC Therapeutics
INDUSTRY