About
Genetic Therapies
Areas of Focus
Categories
Gene Therapy, RNA & Peptide TherapyNJ, NY, PA
Clinical Trials (6)
View allTotal Trials
6
As Lead Sponsor
6
As Collaborator
0
Total Enrollment
145
By Phase
PHASE1/PHASE2: 2PHASE1: 1
By Status
COMPLETED: 2TERMINATED: 2RECRUITING: 1ACTIVE_NOT_RECRUITING: 1
Clinical Trials Pipeline6 trials
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Phase 1/2
Phase 2/3
N/A
2018
2019
2020
2021
2022
2023
2024
2025
2026
2027
2028
2029
2030
Today
Hover over trial bars to see details
Recent Trials
NCT05898620Lead Sponsor
A Novel, Regulated Gene Therapy (NGN-401) Study for Females With Rett Syndrome
PHASE1/PHASE2Recruiting
14 participants
Started: Jun 13, 2023 · Completed: Oct 31, 2029
NCT05228145Lead Sponsor
Gene Therapy Study for Children With CLN5 Batten Disease
PHASE1/PHASE2Active, not recruiting
6 participants
Started: Jan 31, 2022 · Completed: Nov 30, 2028
NCT04659629Lead Sponsor
NL-201 Monotherapy and in Combination With Pembrolizumab in Patients With Relapsed or Refractory Cancer
PHASE1Completed
59 participants
Started: Apr 26, 2021 · Completed: Aug 15, 2024
NCT03810508Lead Sponsor
A Natural History Study of Charcot-Marie-Tooth 4J (CMT4J)
N/ATerminated
21 participants
Started: Jul 18, 2019 · Completed: Feb 15, 2022
NCT03853876Lead Sponsor
A Natural History Study of Aspartylglucosaminuria
N/ATerminated
8 participants
Started: Apr 18, 2019 · Completed: Mar 17, 2022
Locations (1)
Headquarters
New York, NY, United States
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