A Natural History Study of Charcot-Marie-Tooth 4J (CMT4J)

TerminatedOBSERVATIONAL
Enrollment

21

Participants

Timeline

Start Date

July 18, 2019

Primary Completion Date

February 15, 2022

Study Completion Date

February 15, 2022

Conditions
Charcot-Marie-Tooth DiseaseHereditary Motor and Sensory Neuropathy IV
Trial Locations (2)

52242

University of Iowa, Iowa City

75390

University of Texas Southwestern, Dallas

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Neurogene Inc.

INDUSTRY

NCT03810508 - A Natural History Study of Charcot-Marie-Tooth 4J (CMT4J) | Biotech Hunter | Biotech Hunter