A Natural History Study of Aspartylglucosaminuria

TerminatedOBSERVATIONAL
Enrollment

8

Participants

Timeline

Start Date

April 18, 2019

Primary Completion Date

October 15, 2020

Study Completion Date

March 17, 2022

Conditions
AspartylglucosaminuriaAspartylglucosamidase (AGA) DeficiencyLysosomal Storage Diseases
Trial Locations (1)

75390

University of Texas Southwestern, Dallas

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Neurogene Inc.

INDUSTRY