A Natural History Study of Neuronal Ceroid Lipofuscinosis Type 5 (CLN5)

CompletedOBSERVATIONAL
Enrollment

37

Participants

Timeline

Start Date

March 13, 2019

Primary Completion Date

May 30, 2024

Study Completion Date

May 30, 2024

Conditions
Ceroid Lipofuscinosis, Neuronal 5
Trial Locations (1)

14642

University of Rochester Medical Center, Rochester

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Neurogene Inc.

INDUSTRY

NCT03822650 - A Natural History Study of Neuronal Ceroid Lipofuscinosis Type 5 (CLN5) | Biotech Hunter | Biotech Hunter