Peptide drug discovery
Total Trials
8
As Lead Sponsor
As Collaborator
0
Total Enrollment
190
NCT05573984
Natural History of PRPF31 Mutation-Associated Retinal Dystrophy
Phase: N/A
Role: Lead Sponsor
Start: Jul 7, 2022
Completion: Feb 28, 2026
NCT05902962
SAD of IVT VP-001 in PRPF31 Mutation-Associated Retinal Dystrophy Subjects
Phase: Phase 1
Start: Apr 20, 2023
Completion: Aug 30, 2025
NCT06140329
Natural History of Autosomal Dominant Optic Atrophy (ADOA), Caused by OPA1 Mutation
Start: Feb 28, 2024
Completion: Mar 10, 2025
NCT06455826
MAD of IVT VP-001 in PRPF31 Mutation-Associated Retinal Dystrophy Subjects (Wallaby)
Start: Jun 13, 2024
Completion: Nov 30, 2025
NCT06461286
SAD of IVT PYC-001 in OPA1 Mutation-Associated Autosomal Dominant Optic Atrophy (Sundew)
Start: Oct 31, 2024
Completion: Aug 31, 2025
NCT06714006
Phase 1 Study to Evaluate the Safety and Tolerability of Intravenously Administered PYC-003
Start: Apr 7, 2025
Completion: Jan 31, 2026
NCT06852963
A Study of Two Doses of VP-001 Administered Intravitreally in Participants with Confirmed PRPF31 Mutation-Associated Retinal Dystrophy Previously Treated with VP001
Phase: Phase 1/2
Start: Jun 1, 2025
Completion: Aug 1, 2027
NCT06970106
Safety of Single and Repeat Dose of PYC-001 Eye Injections in People With Autosomal Dominant Optic Atrophy
Start: Sep 30, 2025
Completion: Jan 1, 2027
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