Phase 1 Study to Evaluate the Safety and Tolerability of Intravenously Administered PYC-003

PHASE1RecruitingINTERVENTIONAL
Enrollment

56

Participants

Timeline

Start Date

April 7, 2025

Primary Completion Date

January 31, 2026

Study Completion Date

January 31, 2026

Conditions
Autosomal Dominant Polycystic Kidney Disease (ADPKD)
Interventions
DRUG

PYC-003

A peptide-phosphorodiamidate morpholino oligonucleotide conjugate administered as a single intravenous infusion

Trial Locations (6)

2145

RECRUITING

Westmead Hospital, Clinical Research Unit, Level 6, B Wing/Building, Hawkesbury Road, Westmead

2170

RECRUITING

Liverpool Hospital, Clinic G-Reception 133, Level 1, Clinical Building, Burnside Drive, Liverpool

3002

NOT_YET_RECRUITING

Doherty Clinical Trials (Satellite site for Sunshine Hospital), Level 2, 2 St Andrews Place, East Melbourne

4101

RECRUITING

Mater Hospital Brisbane, South Brisbane

4125

RECRUITING

South Coast Renal, Brockway House, Level 1, Suite 8, 82-86 Queen Street,, Southport

6027

RECRUITING

Linear Clinical Research, Joondalup

Sponsors

Lead Sponsor

All Listed Sponsors
lead

PYC Therapeutics

INDUSTRY

NCT06714006 - Phase 1 Study to Evaluate the Safety and Tolerability of Intravenously Administered PYC-003 | Biotech Hunter | Biotech Hunter