Natural History of PRPF31 Mutation-Associated Retinal Dystrophy

Active, not recruitingOBSERVATIONAL
Enrollment

50

Participants

Timeline

Start Date

July 7, 2022

Primary Completion Date

February 28, 2026

Study Completion Date

February 28, 2026

Conditions
Retinitis PigmentosaEye Diseases, HereditaryRetinal DystrophiesRetinal Dystrophy RodRetinal Dystrophy Rod Progressive
Trial Locations (7)

6009

Lions Eye Institute, Nedlands

32209

University of Florida Health, Jacksonville

48105

University of Michigan Kellogg Eye Center, Ann Arbor

75321

Retina Foundation of the Southwest, Dallas

94143

University of California San Francisco, San Francisco

97239

Oregon Health and Science University - Casey Eye Institute, Portland

Unknown

Centre For Eye Research Australia (CERA) - Retinal Gene Therapy Unit, East Melbourne

Sponsors

Lead Sponsor

All Listed Sponsors
lead

PYC Therapeutics

INDUSTRY

NCT05573984 - Natural History of PRPF31 Mutation-Associated Retinal Dystrophy | Biotech Hunter | Biotech Hunter