Safety of Single and Repeat Dose of PYC-001 Eye Injections in People With Autosomal Dominant Optic Atrophy

PHASE1/PHASE2RecruitingINTERVENTIONAL
Enrollment

21

Participants

Timeline

Start Date

September 30, 2025

Primary Completion Date

December 1, 2026

Study Completion Date

January 1, 2027

Conditions
OPA1 Gene MutationAutosomal Dominant Optic AtrophyHereditary Optic AtrophiesKjer Optic Atrophy
Interventions
DRUG

PYC-001

PYC-001 is a peptide-phosphorodiamidate morpholino oligonucleotide administered intravitreally

Trial Locations (2)

2000

RECRUITING

Save Sight Institute - Sydney Eye Hospital, Sydney

Unknown

RECRUITING

Cerulea Clinical Trials, East Melbourne

Sponsors

Lead Sponsor

All Listed Sponsors
lead

PYC Therapeutics

INDUSTRY