Defunct Company
Total Trials
5
As Lead Sponsor
As Collaborator
0
Total Enrollment
41
NCT03952156
Gene Therapy Clinical Study in Adult PKU
Phase: Phase 1/2
Role: Lead Sponsor
Start: Jun 10, 2019
Completion: Aug 1, 2023
NCT04348708
Long-Term Follow Up Study of Subjects Previously Administered HMI 102
Phase: N/A
Start: Aug 19, 2020
Completion: Dec 1, 2026
NCT04768348
Natural History Clinical Study in Adult PKU
Start: Apr 20, 2021
NCT05222178
Safety and Efficacy of HMI-103 in Participants With Classical PKU Due to PAH Deficiency
Phase: Phase 1
Start: Jun 3, 2022
Completion: Sep 14, 2023
NCT05238324
Safety and Efficacy of HMI-203 in ERT-Treated Adults With MPS II
Start: Sep 8, 2022
Completion: Jan 31, 2029