NCT04348708View on ClinicalTrials.gov

Long-Term Follow Up Study of Subjects Previously Administered HMI 102

Enrolling by invitationOBSERVATIONAL
Enrollment

21

Participants

Timeline

Start Date

August 19, 2020

Primary Completion Date

January 30, 2026

Study Completion Date

December 1, 2026

Conditions
PhenylketonuriaPAH Deficiency
Interventions
GENETIC

HMI-102

HMI-102 is an AAVHSC15 vector containing a functional copy of the human PAH gene

Trial Locations (2)

10029

Icahn School of Medicine at Mount Sinai, New York

02115

Boston Children's Hospital, Boston

Sponsors
All Listed Sponsors
lead

Homology Medicines, Inc

INDUSTRY