Characterizing Perceived Physical Fatigability in Nusinersen-treated SMA

RecruitingOBSERVATIONAL
Enrollment

45

Participants

Timeline

Start Date

April 24, 2025

Primary Completion Date

December 7, 2026

Study Completion Date

February 26, 2027

Conditions
Spinal Muscular Atrophy
Interventions
OTHER

Observational

Observational

Trial Locations (1)

10032

RECRUITING

Columbia University Irving Medical Center, New York

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Biogen

INDUSTRY

lead

Columbia University

OTHER