A Real World Effectiveness Study of Pegcetacoplan in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)

RecruitingOBSERVATIONAL
Enrollment

200

Participants

Timeline

Start Date

June 26, 2023

Primary Completion Date

August 15, 2026

Study Completion Date

August 15, 2029

Conditions
Paroxysmal Nocturnal Hemoglobinuria
Interventions
DRUG

Pegcetacoplan

Pegcetacoplan will be prescribed according to the label in patients with PNH.

Trial Locations (75)

1020

ACTIVE_NOT_RECRUITING

CHU Brugmann-Site Horta, Brussels

33604

RECRUITING

CHU de Bordeaux - Hôpital Haut-Lévêque, Pessac

Unknown

RECRUITING

Liverpool Hospital, Liverpool

RECRUITING

Calvary Mater Newcastle, Waratah

RECRUITING

Sunshine Coast University Hospital, Birtinya

ACTIVE_NOT_RECRUITING

AZ Sint-Jan, Bruges

RECRUITING

Centre Hospitalier Universitaire de Liege, Liège

ACTIVE_NOT_RECRUITING

AZ Turnhout - Campus Sint-Elisabeth, Turnhout

RECRUITING

University Health Network, Toronto

ACTIVE_NOT_RECRUITING

Hopital Maisonneuve-Rosemont d/b/a CIUSSS de l'Est-de-l'Île-de-Montréal, Montreal

RECRUITING

Fakultni nemocnice Brno, Brno

RECRUITING

Ustav hematologie a krevni transfuze, Prague

RECRUITING

Helsingin yliopistollinen keskussairaala, Helsinki

RECRUITING

CHU Nice - Hôpital de l'Archet 1, Nice

RECRUITING

Hopital Foch, Suresnes

RECRUITING

CHU de Grenoble - Hôpital Albert Michallon, Grenoble

RECRUITING

CHU de Nantes - Hotel Dieu, Nantes

RECRUITING

CHU de Nancy - Hôpital de Brabois Adultes, Vandœuvre-lès-Nancy

RECRUITING

Hopital Claude Huriez - CHRU Lille, Lille

RECRUITING

Hôpital Saint-Louis, La Defense

RECRUITING

Centre Hospitalier Lyon Sud, Pierre-Bénite

NOT_YET_RECRUITING

CHU Poitiers, Poitiers

ACTIVE_NOT_RECRUITING

Alb-Fils-Kliniken GmbH, Goettigen

ACTIVE_NOT_RECRUITING

Studienzentrum Aschaffenburg, Aschaffenburg

RECRUITING

Universitaetsklinikum Frankfurt Goethe-Universitaet, Frankfurt am Main

ACTIVE_NOT_RECRUITING

Universitaetsklinikum Giessen und Marburg GmbH Standort Giessen, Giessen

RECRUITING

Dres Ballo und Dr. Böck, Offenbach

RECRUITING

Universitaetsklinikum Essen, Essen

ACTIVE_NOT_RECRUITING

Universitaetsklinikum Leipzig AoeR, Leipzig

RECRUITING

Praxis Fenchel Saalfeld, Saalfeld

NOT_YET_RECRUITING

MV Zentrum für Onkologie und Hämatologie, Cologne

NOT_YET_RECRUITING

Evangelismos Hospital, Athens

RECRUITING

"University General Hospital Attikon", Athens

RECRUITING

University General Hospital of Larissa, Larissa

NOT_YET_RECRUITING

G Papanikolaou General Hospital, Thessaloniki

RECRUITING

"General Hospital of Thessaloniki IPPOKRATEIO", Thessaloniki

RECRUITING

DPC - Orszagos Hematologiai es Infektologiai Intezet, Budapest

RECRUITING

Semmelweis Egyetem, Budapest

RECRUITING

Semmelweis University, Budapest

RECRUITING

Azienda Ospedaliero Universitaria Consorziale Policlinico di Bari, Bari

RECRUITING

Ospedale San Bassiano, Bassano del Grappa

NOT_YET_RECRUITING

Irccs Aou Di Bologna- Pol. Di S.Orsola, Bologna

NOT_YET_RECRUITING

Ospedale Oncologico Armando Businco, Cagliari

NOT_YET_RECRUITING

Azienda Ospedaliera Universitaria Careggi, Florence

RECRUITING

Fondazione IRCCS CA' Granda Ospedale Maggiore Policlinico, Milan

RECRUITING

Ospedale San Raffaele, Milan

RECRUITING

Ospedale Maggiore della Carità, Novara

RECRUITING

Grande Ospedale Metropolitano - Presidio Morelli, Reggio Calabria

RECRUITING

Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma

RECRUITING

Università di Roma La Sapienza, Rome

NOT_YET_RECRUITING

Azienda Ospedaliero-Universitaria Città della Salute e della Scienza di Torino, Torino

NOT_YET_RECRUITING

Uniwersytecki Szpital Kliniczny w Bialymstoku, Bialystok

NOT_YET_RECRUITING

Szpital Uniwersytecki nr 2 im. dr J. Biziela w Bydgoszczy, Bydgoszcz

NOT_YET_RECRUITING

Uniwersyteckie Centrum Kliniczne, Gdansk

NOT_YET_RECRUITING

SPZOZ Szpital Uniwersytecki w Krakowie, Krakow

RECRUITING

WWCOiT in Lodz, Oddział Hematologii i Transplantologii, Lodz

NOT_YET_RECRUITING

Uniwersytecki Szpital Kliniczny nr 1 w Lublinie, Lublin

NOT_YET_RECRUITING

Warszawski Uniwersytet Medyczny, Warsaw

NOT_YET_RECRUITING

Prince Faisal Bin Bandar Cancer Center, Buraidah

NOT_YET_RECRUITING

King Faisal Specialist Hospital & Research Center, Jeddah

RECRUITING

King Faisal Specialist Hospital and Research Center - Madinah, Riyadh

RECRUITING

King Faisal Specialist Hospital and Research Center - Riyadh, Riyadh

RECRUITING

ICO Badalona - Hospital Universitari Germans Trias i Pujol, Badalona

RECRUITING

Hospital de Cruces, Barakaldo

RECRUITING

Hospital Clinic de Barcelona, Barcelona

RECRUITING

Hospital Universitari Vall d'Hebron, Barcelona

ACTIVE_NOT_RECRUITING

Hospital de Basurto, Bilbao

RECRUITING

Hospital Universitario Donostia, Donostia / San Sebastian

RECRUITING

Hospital Universitario Virgen de la Nieves, El Palmar

RECRUITING

Hospital Universitario de Gran Canaria Dr. Negrin, Las Palmas de Gran Canaria

RECRUITING

Hospital Lucus Augusti, Lugo

RECRUITING

Hospital Regional Universitario de Malaga, Málaga

RECRUITING

Hospital Universitario Central de Asturias, Oviedo

RECRUITING

Complejo Hospitalario Universitario de Santiago, Santiago de Compostela

RECRUITING

King's College Hospital, London

Sponsors
All Listed Sponsors
collaborator

Iqvia Pty Ltd

INDUSTRY

lead

Swedish Orphan Biovitrum

INDUSTRY