A Study to Evaluate the Efficacy and Safety of Pegcetacoplan in Patients With Cold Agglutinin Disease (CAD)

PHASE3CompletedINTERVENTIONAL
Enrollment

24

Participants

Timeline

Start Date

October 20, 2022

Primary Completion Date

May 27, 2024

Study Completion Date

September 11, 2024

Conditions
Cold Agglutinin Disease
Interventions
DRUG

Pegcetacoplan

Pegcetacoplan taken twice weekly as subcutaneous injection

Trial Locations (44)

2930

Algemeen Ziekenhuis Klina, Brasschaat

3000

UZ Gasthuisberg, Leuven

4000

CHU de Liège, Liège

10021

Weill Cornell Medicine / NewYork Presbyterian Hospital, New York

25123

ASST degli Spedali Civili di Brescia_Presidio Ospedaliero di Brescia_U.O. Ematologia, Brescia

27858

East Carolina University Division of Hematology/ Oncology, Greenville

33014

Lakes Research, Miami Lakes

45147

Universitätsklinikum Essen Klinik f. Hämatologie - Westdeutsches Tumorzentrum, Essen

52242

University of Iowa Hospitals & Clinics - The Hemophilia Treatment Center (HTC), Iowa City

83100

A.O.R.N. S.G. Moscati di Avellino, Avellino

89133

"Grande Ospedale Metropolitano Bianchi - Melacrino - Morellii", Reggio Calabria

90146

"Azienda Ospedaliera Ospedali Riuniti Villa Sofia-Cervello", Palermo

90603

The Oncology Institute of Hope and Innovation, Whittier

5650871

Osaka University Hospital, Osaka

9208530

Ishikawa Prefectural Central Hospital, Kanazawa

Unknown

Medical University, Vienna

St. Michael's Hospital, Toronto

Helsinki University Hospital - Comprehensive Cancer Center, Helsinki

"LTD Medinvest Institute of Hematology and Transfusiology ", Tbilisi

Ltd M. Zodelava Hematology Centre, Tbilisi

Institut f. Transfusionsmedizin - Universität Ulm, Ulm

Semmelweis Egyetem, Budapest

"FOND IRCCS Cà Granda Ospedale Maggiore Policlinico, Milan

AOU Maggiore della Carità SCDU Ematologia, Novara

Fukushima Medical University Hospital, Fukushima

University of Tsukuba Hospital, Ibaraki

Shinshu University Hospital, Nagano

Amsterdam UMC, Amsterdam

Haukeland University Hospital, Bergen

Sykehuset Østfold Kalnes, Grålum

St Olavs Hospital, Avdeling for blodsykdommer, Trondheim

Hospital Clinic de Barcelona, Barcelona

Hospital Universitario de Gran Canaria Dr. Negrin, Las Palmas de Gran Canaria

Hospital Clínico Universitario de Salamanca, Madrid

Hospital Universitario Infanta Leonor, Madrid

Hospital Universitario La Paz, Madrid

Hospital Universitario Virgen del Rocio, Seville

Hospital Universitario y Politecnico La Fe, Valencia

Cancer Clinical Trials Unit, Haematology -University College London -, London

Churchill Hospital, Oxford

480-1195

Aichi Medical University Hospital, Nagakute

LS9 7TF

St James' University Hospital, Leeds

E1 2ES

Royal London Hospital, London

NG5 1PB

Russell Centre for Clinical Haematology, Nottingham

Sponsors
All Listed Sponsors
lead

Swedish Orphan Biovitrum

INDUSTRY