45
Participants
Start Date
January 21, 2022
Primary Completion Date
June 14, 2027
Study Completion Date
June 14, 2027
Nusinersen
Administered as specified in the treatment arm
Ospedale Pediatrico Bambino Gesù, Rome
Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma
Semmelweis Egyetem, Budapest
UZ Leuven, Leuven
Hospital Sant Joan de Deu, Esplugues de Llobregat
UZ Gent, Ghent
Columbia University, New York
Ospedale S G Battista Molinette, Torino
Charité - Campus Virchow-Klinikum, Berlin
University of Pennsylvania, Philadelphia
Georgetown University, Washington D.C.
Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan
Fondazione Serena Onlus - Centro Clinico Nemo, Milan
Children's Hospital of The King's Daughters, Norfolk
Wake Forest University - School of Medicine - Central, Winston-Salem
Rare Disease Research, LLC, Atlanta
Universitaetsklinikum Giessen und Marburg GmbH, Giessen
The Ohio State, Columbus
Universitaetsklinikum Essen, Essen
Universitaetsklinikum Essen, Essen
Hospital Universitari i Politecnic La Fe, Valencia
Memorial Healthcare, Owosso
University of Iowa Stead Family Children's Hospital, Iowa City
University of Wisconsin, Madison
Universitaetsklinikum Heidelberg, Heidelberg
Arkansas Children's Hospital, Little Rock
Neurology Rare Disease Center, Denton
The University of Texas Health Science Center at Houston, Houston
Klinikum rechts der Isar der TU Muenchen, Munich
Barrow Neurological Institute, Phoenix
Universitaetsklinikum Ulm, Ulm
Loma Linda University Children's Hospital, Loma Linda
Stanford Neuroscience Health Center, Palo Alto
University of Washington Medical Center, Seattle
Hospital das Clinicas - FMUSP, São Paulo
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
Boston Children's Hospital, Boston
Hospital de Clínicas de Porto Alegre, Porto Alegre
Yokohama City University Hospital, Yokohama
NHO Osaka Toneyama Medical Center, Toyonaka-shi
Szpital Specjalistyczny im. L.Rydygiera w Krakowie, Krakow
Instytut Centrum Zdrowia Matki Polki, Lodz
Samodzielny Publiczny Centralny Szpital Kliniczny, Warsaw
Uniwersytecki Szpital Kliniczny im. Jana Mikulicza Radeckiego we Wroclawiu, Wroclaw
Lead Sponsor
Biogen
INDUSTRY