286
Participants
Start Date
February 11, 2022
Primary Completion Date
October 31, 2025
Study Completion Date
February 28, 2030
Mitapivat
Mitapivat tablets
Mitapivat-matching placebo
Placebo to match 50 mg or 100 mg tablets
Mitapivat-matching placebo
Placebo to match 100 mg tablets
Hôpital Erasme, Anderlecht
Nini Hospital, Tarablus
ZAS Cadix, Antwerp
Universitair Ziekenhuis Antwerpen, Edegem
CHR de la Citadelle, Liège
Clinique CHC MontLégia, Liège
King Khalid University Hospital, Riyadh
Hopitaux de La Timone, Marseille
Ziv Medical Center, Safed
Ente Ospedaliero Ospedali Galliera, Genoa
HaEmek Medical Center, Afula
MedStar Washington Hospital Center, Washington D.C.
National Heart Lung and Blood Institute, Bethesda
East Carolina University - Brody School of Medicine, Greenville
Institut Universitaire du Cancer de Toulouse - Oncopole, Toulouse
Rambam Medical Center, Haifa
Hôpital Pellegrin, CHU de Bordeaux, Bordeaux
Sylvester Comprehensive Cancer Center-Miami, Miami
Southern Specialty Clinic, Flowood
Kemri Usamru, Kisumu
Kondele Children's Hospital, Kisumu
Victoria Biomedical Research Institute (VIBRI), Kisumu
Azienda Ospedaliero Universitaria Di Modena Policlinico, Modena
Universitätsklinikum Essen, Essen
Children's Hospital of Michigan, Detroit
Hôpital Européen Georges Pompidou, Paris
Texas Children's Hospital, Houston
"A.O.R.N. A. Cardarelli", Napoli
AOU dell'Università degli Studi della Campania Luigi Vanvitelli, Napoli
Cure 4 The Kids Foundation, A Division of Roseman University of Health Sciences, Las Vegas
Azienda Ospedaliera Ospedali Riuniti Villa Sofia-Cervello, Palermo
Universitätsklinikum Regensburg, Regensburg
CHU Hôpital Henri Mondor, Créteil
Children's Hospital Oakland, Oakland
CHU Guadeloupe, Pointe à Pitre
Seattle Cancer Care Alliance, University of Washington, Seattle
Lagos University Teaching Hospital, Surulere
National Hospital Abuja, Abuja
University of Abuja Teaching Hospital, Abuja
University of California San Diego, La Jolla
UCLA Health, Los Angeles
University of Connecticut Health Center, Farmington
Children's National Hospital, Washington D.C.
University of Chicago Medical Center, Chicago
Riley Hospital For Children, Indianapolis
LSU Health Sciences Center - Shreveport, Shreveport
Kaiser Permanente - Largo Medical Center, Largo
Massachusetts General Hospital, Boston
Boston Children's Hospital, Boston
Boston Medical Center & Boston University School of Medicine, Boston
University of Michigan, Ann Arbor
Mississippi Center for Advanced Medicine, Madison
Penn Medicine - University of Pennsylvania Health System, Philadelphia
St. Christopher's Hospital for Children, Philadelphia
Lifespan at Rhode Island Hospital, Providence
University of Texas Health Science Center of Houston, Houston
Virginia Commonwealth University, Richmond
Multihemo Servicos Medicos S/A, Recife
Hospital de Clinicas de Porto Alegre (HCPA) - PPDS, Porto Alegre
Hospital Sao Lucas Da Pontificia Universidade Catolica Do Rio Grande Do Sul (PUCRS), Porto Alegre
Hospital de Clínicas da Unicamp, Campinas
Hospital Das Clínicas da Faculdade de Medicina de Ribeirão Preto - USP, Ribeirão Preto
Praxis Pesquisa Medica, Santo André
Hacettepe University, Ankara
HEMORIO Instituto Nacional de Hematologia, Rio de Janeiro
Hospital das Clínicas da Faculdade de Medicina da Universidad de São Paulo, São Paulo
McMaster University - St. Joseph's Healthcare Hamilton, Hamilton
University Health Network, Toronto
CHU Montreal, Montreal
McGill University Health Center, Montreal
IRCCS Ospedale Pediatrico Bambino Gesù - INCIPIT - PIN, Rome
KEMRI CRDR Clinical Research Clinic Nairobi, Nairobi
KEMRI/CRDR Siaya Clinical Research Annex, Nairobi
Strathmore University, Nairobi
Gertrude's Children's Hospital, Nairobi
American University of Beirut Medical Center, Beirut
American University of Beirut Medical Center, Beirut
Hammoud Hospital University Medical Center, Sidon
Erasmus MC, Rotterdam
Universitair Medisch Centrum Utrecht, Utrecht
Sultan Qaboos University Hospital, Hematology Department, COM&HS, Muscat
King Abdullah International Medical Research Center, Riyadh
Acibadem Adana Hospital, Seyhan
Evelina Children's Hospital, London
Guy's and St Thomas' NHS Foundation Trust, London
Cambridge University Hospitals NHS Foundation Trust, Cambridge
King's College Hospital NHS Foundation Trust, London
Hammersmith Hospital, London
University College London Hospitals (UCLH), London
Manchester Royal Infirmary, Manchester University NHS Foundation Trust, Manchester
Lead Sponsor
Agios Pharmaceuticals, Inc.
INDUSTRY