Evaluate Efficacy, Safety and Tolerability, PK and PD of Emapalumab in Children and Adults With MAS in Still's or SLE

PHASE3CompletedINTERVENTIONAL
Enrollment

33

Participants

Timeline

Start Date

December 15, 2021

Primary Completion Date

June 30, 2024

Study Completion Date

June 4, 2025

Conditions
Macrophage Activation SyndromeSecondary Hemophagocytic LymphohistiocytosisStill DiseaseSystemic Lupus ErythematosusSJIAAOSDMAS
Interventions
DRUG

Emapalumab

Emapalumab iv infusion

Trial Locations (44)

15213

UPMC Children's Hospital of Pittsburgh, Pittsburgh

30329

Children's Healthcare of Atlanta, Atlanta

32610

University of Florida, Gainesville

35233

UAB Hospital, Birmingham

43205

Nationwide Children's Hospital, Abigail Wexner Research Institute, Columbus

44308

Akron Children's Hospital, Akron

45229

Cincinnati Children's Hospital Medical Center, Cincinnati

55455

University of Minnesota Masonic Children's Hospital, Minneapolis

90095

UCLA Health, Los Angeles

Unknown

Universitair Ziekenhuis Leuven, Leuven

Alberta Children's Hospital, Calgary

University of Calgary, Calgary

Centre Hospitalier de l'Université de Montréal, Montreal

Centre Hospitalier Universitaire Sainte-Justine, Montreal

Hospital for sick children, Toronto

Beijing Children's Hospital, Beijing

Beijing Friendship Hospital, Beijing

Children's Hospital of Fudan University, Shanghai

Fakultní nemocnice Olomouc, Olomouc

Vseobecna Fakultni Nemocnice v Praze, Prague

Hôpital Claude Huriez, Lille

Hôpital De La Conception, Marseille

Hôpital Necker-Enfants Malades, Paris

Hôpital Universitaire Pitié Salpêtrière, Paris

Charité Universitätsmedizin, Berlin

Universitätsklinikum Heidelberg, Heidelberg

IRCCS G. Gaslini, Genova

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan

Ospedale Pediatrico Bambino Gesù, Roma

IRCCS - Materno-Infantile Burlo Garofolo, Trieste

St. Marianna University School of Medicine Hospital, Kawasaki

Osaka Medical and Pharmaceutical University Hospital, Takatsuki

Tokyo Medical and Dental University Hospital, Tokyo

Yokohama City University Hospital, Yokohama

UMC Utrecht, Utrecht

Szpital Specjalistyczny im. J. Dietla w Krakowie, Krakow

Wojewódzki Specjalistyczny Szpital Dziecięcy im. św. Ludwika w Krakowie, Krakow

Ortopedyczno - Rehabilitacyjny Szpital Kliniczny im. Wiktora Degi Uniwersytetu Medycznego im. Karola Marcinkowskiego w Poznaniu, Poznan

Hospital Sant Joan de Déu, Barcelona

Hospital Universitario La Paz, La Paz

Hospital Universitario, La Paz

Hospital Universitari i Politècnic La Fe, Valencia

Great Ormond Street Hospital, London

Imperial College Healthcare NHS Trust, London

Sponsors
All Listed Sponsors
lead

Swedish Orphan Biovitrum

INDUSTRY