Pyruvate Kinase (PK) Deficiency Global Longitudinal Registry: Patient-Reported Outcomes (PRO)

TerminatedOBSERVATIONAL
Enrollment

15

Participants

Timeline

Start Date

July 2, 2021

Primary Completion Date

June 30, 2023

Study Completion Date

June 30, 2023

Conditions
Pyruvate Kinase DeficiencyPyruvate Kinase Deficiency AnemiaAnemiaAnemia, Hemolytic
Trial Locations (5)

20122

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, Milan

28009

Hospital Infantil Universitario Niño Jesus - PIN, Madrid

02114

Massachusetts General Hospital, Boston

3508 GA

Universitair Medisch Centrum Utrecht, Utrecht

W12 0HS

Hammersmith Hospital, London

Sponsors
All Listed Sponsors
lead

Agios Pharmaceuticals, Inc.

INDUSTRY