A Study Evaluating the Efficacy and Safety of Mitapivat in Participants With Transfusion-Dependent Alpha- or Beta-Thalassemia (α- or β-TDT)

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

258

Participants

Timeline

Start Date

November 30, 2021

Primary Completion Date

April 11, 2024

Study Completion Date

June 30, 2029

Conditions
Transfusion-dependent Alpha-ThalassemiaTransfusion-dependent Beta-Thalassemia
Interventions
DRUG

Placebo Matching Mitapivat

Tablets

DRUG

Mitapivat

Tablets

Trial Locations (75)

100

National Taiwan University Hospital, Taipei

1130

Acibadem Adana Hospital, Adana

1756

SHATHD Sofia, Sofia

2100

Rigshospitalet, Hovedstaden

2500

"MHAT Dr. Nikola Vasiliev AD", Kyustendil

4002

"UMHAT Sveti Georgi EAD", Plovdiv

5800

"UMHAT Dr. Georgi Stranski Pleven", Pleven

6000

"UMHAT Prof. Dr. Stoyan Kirkovich", Stara Zagora

9999

Chronic Care Center, Beirut

10043

A.O.U. San Luigi Gonzaga, Orbassano

10400

Phramongkutklao Hospital, Bangkok

Ramathibodi Hospital, Bangkok

10700

Faculty of Medicine Siriraj Hospital, Bangkok

10990

Hospital Pulau Pinang, Pulau Pinang

11527

Children's Hospital Agia Sophia, National and Kapodistrian University of Athens Medical School, Athens

13353

Charité - UB - CVK - Medizinische Klinik, Berlin

13385

CHU Hôpital de la Timone, Marseille

14611

King Abdullah International Medical Research Center, Riyadh

16128

Ente Ospedaliero Ospedali Galliera, Genova

19104

Penn Medicine - University of Pennsylvania Health System, Philadelphia

20122

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, Milan

25100

Hospital Tengku Ampuan Afzan, Kuantan

26504

University General Hospital of Patras, Achaia

28046

Hospital Universitario La Paz, Madrid

30120

Hospital Universitario Virgen Arrixaca, Murcia

34093

Istanbul University Faculty of Medicine, Fatih

35040

Ege University Faculty of Medicine, Bornova

40000

Srinagarind Hospital, Khon Kaen University, Khon Kaen

41013

Hospital Universitario Virgen del Rocío, Seville

41124

A.O.U Di Modena, Modena

44124

Ospedale Sant'Anna, Ferrara

45122

Universitätsklinikum Essen, Essen

50200

Maharaj Nakorn Chiang Mai Hospital, Chiang Mai

50300

Hospital Tunku Azizah, Kuala Lumpur

65000

Naresuan University Hospital, Mueang Phitsanulok

68000

Hospital Ampang, Pandan Indah

69003

Hôpital Edouard Herriot, CHU de Lyon, Lyon

72100

"Ospedale A. Perrino - Brindisi", Brindisi

75015

Hôpital Necker Enfants Malades, Paris

80100

Hospital Sultanah Aminah Johor Bahru, Johor Bahru

80138

AOU L. Vanvitelli Universita degli Studi della Campania Luigi Vanvitelli, Napoli

88586

Hospital Queen Elizabeth, Kota Kinabalu, Kota Kinabalu

90210

King Khalid University Hospital, Riyadh

92093

San Diego Hospital, UC San Diego Health, La Jolla

93586

Hospital Umum Sarawak, Kuching

94010

CHU Hôpital Henri Mondor, Créteil

98101

Seattle Cancer Care Alliance, University of Washington, Seattle

85016-7710

Phoenix Children's Hospital, Phoenix

94609-1809

Children's Hospital Oakland, Oakland

94304-1601

Stanford Medicine, Palo Alto

02115

Boston Children's Hospital, Boston

48201-2196

Children's Hospital of Michigan, Detroit

10065-4870

Weill Cornell Medical Center, New York

27710-3038

Duke University Medical Center, Durham

14051-260

Hospital Das Clínicas da Faculdade de Medicina de Ribeirão Preto - USP, Ribeirão Preto

04006-002

GSH Banco de Sangue de São Paulo, São Paulo

T2N 2T9

Foothills Medical Centre, Calgary

M5G 2C4

Toronto General Hospital, University Health Network, Toronto

04103

Universitätsklinikum Leipzig, Leipzig

115 26

Laiko General Hospital, Athens

455 00

University Hospital of Ioannina, Ioannina

546 42

Ippokrateio General Hospital, Thessaloniki

09121

Ospedale Pediatrico Microcitemico, Cagliari

05460

Hospital Sultanah Bahiyah, Alor Star

1105 AZ

Amsterdam Universitair Medisch Centrum, Locatie AMC, Amsterdam

3584 CX

Universitair Medisch Centrum Utrecht, Utrecht

3015 AA

Erasmus MC, Westzeedijk 353

08035

Hospital Universitario Vall d'Hebron, Barcelona

Unknown

King Chulalongkorn Memorial Hospital, Pathum Wan

Hacettepe University, Mersin

Burjeel Medical City, Abu Dhabi

07059

Akdeniz University Faculty of Medicine, Antalya

01330

Çukurova University, Balcalı

W12 0HS

Imperial College Healthcare NHS Trust - Hammersmith Hospital, London

WC1E 6BT

University College London, London

Sponsors
All Listed Sponsors
lead

Agios Pharmaceuticals, Inc.

INDUSTRY