258
Participants
Start Date
November 30, 2021
Primary Completion Date
April 11, 2024
Study Completion Date
June 30, 2029
Placebo Matching Mitapivat
Tablets
Mitapivat
Tablets
National Taiwan University Hospital, Taipei
Acibadem Adana Hospital, Adana
SHATHD Sofia, Sofia
Rigshospitalet, Hovedstaden
"MHAT Dr. Nikola Vasiliev AD", Kyustendil
"UMHAT Sveti Georgi EAD", Plovdiv
"UMHAT Dr. Georgi Stranski Pleven", Pleven
"UMHAT Prof. Dr. Stoyan Kirkovich", Stara Zagora
Chronic Care Center, Beirut
A.O.U. San Luigi Gonzaga, Orbassano
Phramongkutklao Hospital, Bangkok
Ramathibodi Hospital, Bangkok
Faculty of Medicine Siriraj Hospital, Bangkok
Hospital Pulau Pinang, Pulau Pinang
Children's Hospital Agia Sophia, National and Kapodistrian University of Athens Medical School, Athens
Charité - UB - CVK - Medizinische Klinik, Berlin
CHU Hôpital de la Timone, Marseille
King Abdullah International Medical Research Center, Riyadh
Ente Ospedaliero Ospedali Galliera, Genova
Penn Medicine - University of Pennsylvania Health System, Philadelphia
Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, Milan
Hospital Tengku Ampuan Afzan, Kuantan
University General Hospital of Patras, Achaia
Hospital Universitario La Paz, Madrid
Hospital Universitario Virgen Arrixaca, Murcia
Istanbul University Faculty of Medicine, Fatih
Ege University Faculty of Medicine, Bornova
Srinagarind Hospital, Khon Kaen University, Khon Kaen
Hospital Universitario Virgen del Rocío, Seville
A.O.U Di Modena, Modena
Ospedale Sant'Anna, Ferrara
Universitätsklinikum Essen, Essen
Maharaj Nakorn Chiang Mai Hospital, Chiang Mai
Hospital Tunku Azizah, Kuala Lumpur
Naresuan University Hospital, Mueang Phitsanulok
Hospital Ampang, Pandan Indah
Hôpital Edouard Herriot, CHU de Lyon, Lyon
"Ospedale A. Perrino - Brindisi", Brindisi
Hôpital Necker Enfants Malades, Paris
Hospital Sultanah Aminah Johor Bahru, Johor Bahru
AOU L. Vanvitelli Universita degli Studi della Campania Luigi Vanvitelli, Napoli
Hospital Queen Elizabeth, Kota Kinabalu, Kota Kinabalu
King Khalid University Hospital, Riyadh
San Diego Hospital, UC San Diego Health, La Jolla
Hospital Umum Sarawak, Kuching
CHU Hôpital Henri Mondor, Créteil
Seattle Cancer Care Alliance, University of Washington, Seattle
Phoenix Children's Hospital, Phoenix
Children's Hospital Oakland, Oakland
Stanford Medicine, Palo Alto
Boston Children's Hospital, Boston
Children's Hospital of Michigan, Detroit
Weill Cornell Medical Center, New York
Duke University Medical Center, Durham
Hospital Das Clínicas da Faculdade de Medicina de Ribeirão Preto - USP, Ribeirão Preto
GSH Banco de Sangue de São Paulo, São Paulo
Foothills Medical Centre, Calgary
Toronto General Hospital, University Health Network, Toronto
Universitätsklinikum Leipzig, Leipzig
Laiko General Hospital, Athens
University Hospital of Ioannina, Ioannina
Ippokrateio General Hospital, Thessaloniki
Ospedale Pediatrico Microcitemico, Cagliari
Hospital Sultanah Bahiyah, Alor Star
Amsterdam Universitair Medisch Centrum, Locatie AMC, Amsterdam
Universitair Medisch Centrum Utrecht, Utrecht
Erasmus MC, Westzeedijk 353
Hospital Universitario Vall d'Hebron, Barcelona
King Chulalongkorn Memorial Hospital, Pathum Wan
Hacettepe University, Mersin
Burjeel Medical City, Abu Dhabi
Akdeniz University Faculty of Medicine, Antalya
Çukurova University, Balcalı
Imperial College Healthcare NHS Trust - Hammersmith Hospital, London
University College London, London
Lead Sponsor
Agios Pharmaceuticals, Inc.
INDUSTRY