194
Participants
Start Date
December 20, 2021
Primary Completion Date
November 13, 2023
Study Completion Date
December 31, 2028
Placebo Matching Mitapivat
Tablets
Mitapivat
Tablets
SHATHD Sofia, Sofia
Rigshospitalet, Copenhagen
"MHAT Dr. Nikola Vasiliev AD", Kyustendil
Thalassemia Centre Dubai, Dubai
Chronic Care Center, Beirut
A.O.U. San Luigi Gonzaga, Orbassano
King Chulalongkorn Memorial Hospital, Pathum Wan
Phramongkutklao Hospital, Bangkok
Ramathibodi Hospital, Bangkok
Faculty of Medicine Siriraj Hospital, Bangkok
Hospital Pulau Pinang, Pulau Pinang
King Abdullah International Medical Research Center, Riyadh
Ente Ospedaliero Ospedali Galliera, Genova
Penn Medicine - University of Pennsylvania Health System, Philadelphia
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan
Hospital Tengku Ampuan Afzan, Kuantan
University General Hospital of Patras, Rio
Hospital Universitario La Paz, Madrid
Hospital Universitario Virgen Arrixaca, Murcia
Istanbul University Faculty of Medicine, Fatih
Ege University Faculty of Medicine, Bornova
King Abdulaziz Hospital - Al Ahsa, Al Mubarraz
Srinagarind Hospital, Khon Kaen University, Khon Kaen
China Medical University, Taiwan, Taichung
Hospital Universitario Virgen del Rocío, Seville
A.O.U Di Modena, Modena
Ospedale Sant'Anna, Ferrara
Maharaj Nakorn Chiang Mai Hospital, Chiang Mai
Hospital Tunku Azizah, Kuala Lumpur
Naresuan University Hospital, Mueang Phitsanulok
Hospital Ampang, Ampang
Hopital Edouard Herriot, CHU de Lyon, Lyon
"Ospedale A. Perrino - Brindisi", Brindisi
Hospital Sultanah Aminah Johor Bahru, Johor Bahru
"A.O.R.N. A. Cardarelli", Napoli
AOU L. Vanvitelli Universita degli Studi della Campania Luigi Vanvitelli, Napoli
Hospital Queen Elizabeth, Kota Kinabalu, Kota Kinabalu
San Diego Hospital, UC San Diego Health, La Jolla
Hospital Umum Sarawak, Kuching
CHU Hôpital Henri Mondor, Créteil
Stanford Medicine, Palo Alto
Massachusetts General Hospital, Boston
Weill Cornell Medical Center, New York
Duke University Medical Center, Durham
Universidade de Caxias do Sul, Caxias do Sul
Hospital das Clínicas da Faculdade de Medicina de Ribeirão Preto - USP, Ribeirão Preto
HEMORIO Instituto Nacional de Hematologia, Rio de Janeiro
Praxis Pesquisa Medica, Santo André
GSH Banco de Sangue de São Paulo, São Paulo
Instituto do Cancer do Estado de São Paulo, Hospital das Clínicas da Faculdade de Medicina da Universidad de São Paulo, São Paulo
Toronto General Hospital, University Health Network, Toronto
Laiko General Hospital, Athens
Children's Hospital Agia Sophia, National and Kapodistrian University of Athens Medical School, Athens
Ippokrateio General Hospital, Thessaloniki
Ospedale Pediatrico Microcitemico, Cagliari
Hospital Sultanah Bahiyah, Alor Star
Erasmus MC, Rotterdam
Universitair Medisch Centrum Utrecht, Utrecht
Hospital Universitario Vall d'Hebron, Barcelona
Acibadem Adana Hospital, Adana
Akdeniz University Faculty of Medicine, Antalya
Çukurova University, Balcalı
Hacettepe University, Mersin
Burjeel Medical City, Abu Dhabi
Cambridge University Hospitals NHS Foundation Trust - Addenbrookes Hospital, Cambridge
Manchester Royal Infirmary, Manchester University NHS Foundation Trust, Manchester
University College London, London
Imperial College Healthcare NHS Trust - Hammersmith Hospital, London
Lead Sponsor
Agios Pharmaceuticals, Inc.
INDUSTRY