182
Participants
Start Date
December 18, 2020
Primary Completion Date
June 30, 2026
Study Completion Date
April 30, 2027
Volixibat
Oral capsules, administered twice daily. Volixibat is an Ileal Bile Acid Transporter (IBAT) inhibitor.
Placebo
Capsules matched to study drug minus active substance
Cliniques Universitaires Saint-Luc, Brussels
Liverpool Hospital, Liverpool
Austin Health, Melbourne
University of the Sunshine Coast, Sippy Downs
Royal Adelaide Hospital, Adelaide
University Hospital Zurich, Zurich
Universitair Ziekenhuis Antwerpen (UZA), Ghent
University Hospital Ghent, Ghent
New York University Langone Health, New York
Weill Cornell Medical College, New York
Columbia University Medical Center - Presbyterian Hospital and Vanderbilt Clinic, New York
Northwell Health, Manhasset
Charité Universtitätsmedizin - Campus Virchow-Klinikum, Berlin
University of Rochester Medical Center - Strong Memorial Hospital, Rochester
University of Pittsburgh Medical Center, Pittsburgh
Einstein Healthcare Network - Einstein Medical Center, Philadelphia
MedStar Georgetown University Hospital, Washington D.C.
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico, Milan
ASST Grande Ospedale Metropolitano Niguarda, Milan
Fondazione IRCCS San Gerardo dei Tintori, Monza
Richmond Community Hospital LLC, Richmond
Bon Secours Liver Institution of Hampton Roads Mary Immaculate Hospital Office, Newport News
Universitätsklinikum Schleswig-Holstein - Campus Kiel, Kiel
Science 37, Inc (Remote-homebased Telemedicine), Morrisville
Duke Health - Duke University Medical Center, Durham
Hospital General Universitario Gregorio Maranon, Madrid
Hannover Medical School, Hanover
University of Miami - Schiff Center for Liver Diseases, Miami
CHU Bordeaux - Haut Lévêque, Pessac
Tampa General Hospital, Tampa
Florida Research Institute, Lakewood Rch
Azienda Ospedale Universita Padova, Padua
Vanderbilt University Medical Center, Nashville
Galen Medical Group, Hixson
Centre Hospitalier Universitaire Grenoble Alpes (CHU Grenoble Alpes), Grenoble
Hillel Yaffe Medical Center, Hadera
Otto-von-Guericke-Universitat Magdeburg, Magdeburg
Southern Therapy and Advanced Research LLC, Jackson
Azienda Ospedaliero-Universitaria di Bologna - Policlinico S. Orsola-Malpighi, Bologna
Cleveland Clinic, Cleveland
Henry Ford Hospital, Detroit
Sheba Medical Center, Ramat Gan
Universitaetsklinikum Bonn, Bonn
Mayo Clinic, Rochester
Centre Hospitalier Universitaire de Lille, Lille
St. Josefs-Hospital Wiesbaden, Wiesbaden
University Hospital Tubingen Medical Clinic, Tübingen
The Liver Institute At Methodist Dallas Medical Center, Dallas
University of Texas Southwestern Medical Center, Dallas
APHP-Hôpital Saint Antoine, Paris
Houston Methodist Hospital, Houston
Liver Associates of Texas, Houston
University of Colorado - Anschutz Medical Campus, Aurora
A.O.U. Federico II, Napoli
University of Utah Health Care, Salt Lake City
Cedars Sinai Medical Center, Los Angeles
Universitaetsklinikum Erlangen, Erlangen
Hadassah Medical Center - Ein Karem, Jerusalem
Southern California Research Center, Coronado
California Pacific Medical Center Research Institute, San Francisco
University of California, Davis, Sacramento
University of Washington - Harborview Medical Center, Seattle
Liver Institute Northwest, Seattle
Galilee Medical Center, Nahariya
Rambam Medical Center, Haifa
Carmel Medical Center, Haifa
Rabin Medical Center, Petah Tikva
Tel Aviv Sourasky Medical Center, Tel Aviv
Shaare Zedek Medical Center, Jerusalem
Beth Israel Deaconess Medical Center, Boston
Hospital Italiano de Buenos Aires, Buenos Aires
Glenny Corp S.A., Ciudad Autónoma Buenos Aires
Hospital El Cruce, San Juan Bautista
Northern Health, Epping
Hospital das Clinicas da UFMG, Belo Horizonte
Hospital Das Clínicas Da Ufg, Goiânia
Hospital de Clinicas de Porto Alegre, Porto Alegre
Escola Bahiana de Medicina e Saude Publica, Salvador
Hospital do Rim e Hipertensao, São Paulo
University of Alberta, Edmonton
McMaster University Hospital, Hamilton
The Ottawa Hospital - General Campus, Ottawa
University Hospital Southampton NHS Foundation Trust, Southampton
University Health Network - Toronto General Hospital, Toronto
University of Calgary, Calgary
London Health Sciences Centre University Hospital, London
McGill University Health Centre - Royal Victoria Hospital, Montreal
Universitatsklinikum Leipzig, Leipzig
Amsterdam UMC - VU Medisch Centrum (VUmc), Amsterdam
Universitair Medisch Centrum Groningen, Groningen
Radboud University Medical Centre (MC), Nijmegen
Erasmus University Medical Center, Rotterdam
Hospital Clinic Barcelona, Barcelona
Royal Free Hospital, London
John Radcliffe Hospital, Oxford
Royal Victoria Hospital, Belfast
University Hospitals Birmingham NHS Foundation Trust - Wellcome Trust Birmingham Clinical Research Facility, Birmingham
Cambridge University Hospitals NHS Foundation Trust - Addenbrooke's Hospital, Cambridge
Lothian NHS Board, Edinburgh
St James' University Hospital Leeds Teaching Hospitals NHS Trust, Leeds
King's College Hospital NHS Foundation Trust, London
The Newcastle upon Tyne Hospitals NHS Foundation Trust - Royal Victoria Infirmary, Newcastle upon Tyne
Nottingham University Hospital NHS Trust, Nottingham
Lead Sponsor
Mirum Pharmaceuticals, Inc.
INDUSTRY