145
Participants
Start Date
March 26, 2020
Primary Completion Date
February 21, 2024
Study Completion Date
May 30, 2024
Nusinersen
Administered as specified in the treatment arm
Semmelweis Egyetem, Budapest
Magyarorszagi Reformatus Egyhaz Bethesda Gyermekkorhaz, Budapest
National Taiwan University Hospital, Taipei
King Faisal Specialist Hospital & Research Center, Riyadh
Tallinn Children's Hospital, Tallinn
Fondazione Serena Onlus - Centro Clinico Nemo, Milan
The Johns Hopkins Hospital, Baltimore
National Guard Health Affairs: King Abdulaziz Medical City, Jeddah
Hospital Universitario La Paz, Madrid
King Fahad Specialist Hospital, Dammam
Universitaetsklinikum Giessen und Marburg GmbH, Giessen
St. Jude Children's Research Hospital, Memphis
Antiguo Hospital Civil de Guadalajara Fray Antonio Alcalde, Guadalajara
Hospital Universitari i Politecnic La Fe, Valencia
Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago
The University of Texas Southwestern Medical Center, Dallas
Universitaetsklinikum Freiburg, Freiburg im Breisgau
Children's Hospital Colorado, Aurora
Kaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City
Stanford Hospital and Clinics, Palo Alto
Peking University First Hospital, Beijing
Hospital Universitario San Ignacio, Bogotá
Russian Children Neuromuscular Center of Veltischev, Moskva
The Children's Hospital of Zhejiang University school of Med_Hangzhou, Hangzhou
Xiangya Hospital, Central South University, Changsha
Guangzhou Woman and Children's Medical Center, Guangzhou
Regional Pediatric Clinical Hospital #1, Yekaterinburg
Hospital Luis Calvo Mackenna, Santiago
Clinica Las Condes, Santiago
Clinica MEDS La Dehesa, Santiago
Boston Children's Hospital, Boston
HC-UFMG - Hospital das Clinicas da Universidade Federal de Minas Gerais, Belo Horizonte
Hospital de Clínicas de Porto Alegre, Porto Alegre
Hospital das Clínicas da Faculdade de Medicina da USP, São Paulo
London Health Sciences Centre (LHSC) - Children's Hospital, London
Fundacion Hospitalaria San Vicente de Paul, Medellín
Fondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma
Kurume University Hospital, Kurume-shi
Hyogo College of Medicine Hospital, Nishinomiya-shi
Tokyo Women's Medical University Hospital, Shinjuku-ku
Saint George University Hospital Medical Center, Beirut
Instituto Nacional de Pediatria, Mexico City
Hospital Infantil de Mexico Federico Gomez, Mexico City
Instytut Pomnik - Centrum Zdrowia Dziecka, Warsaw
Hospital Sant Joan de Deu, Esplugues Del Llobregat
Lead Sponsor
Biogen
INDUSTRY