93
Participants
Start Date
July 9, 2019
Primary Completion Date
September 1, 2022
Study Completion Date
September 1, 2022
Maralixibat
Maralixibat oral solution (up to 600 mcg/kg) orally twice daily for 26 weeks.
Placebo
Placebo matching to maralixibat orally twice daily for 26 weeks.
Semmelweis Egyetem - Altalanos Orvostudomanyi Kar (SE AOK), Budapest
The Children's Hospital at Montefiore Yeshiva University - Montefiore Medical Center, New York
UPMC Children's Hospital of Pittsburgh, Pittsburgh
Medical University of South Carolina, Charleston
CHU de Toulouse - Hôpital des Enfants, Toulouse
Advent Health, Orlando
Cleveland Clinic - Pediatric Institute, Cleveland
Cincinnati Children's Hospital, Cincinnati
University of Texas - UT Southwestern Medical Center, Dallas
University of Texas, Health Science Center San Antonio, San Antonio
Children's Hospital Los Angeles CHLA, Los Angeles
Seattle Children's Hospital, Seattle
Medstar Georgetown University Hospital, Washington D.C.
Hospital Italiano de Buenos Aires, Buenos Aires
Medizinische Universität Wien, Universitätsklinik für Kinder- und Jugendheilkunde, Vienna
Universite Catholique de Louvain (UCLouvain) - Cliniques Universitaires Saint-Luc, Brussels
Sociedade Beneficente de Senhoras Hospital Sírio-Libanês, São Paulo
University of Alberta - Women and Children's Health Research Institute, Edmonton
Fundacion Cardioinfantil - Departamento de Investigaciones, Bogotá
Hospices Civils de Lyon - Hopital Femme Mere Enfant Service de Gastroenterologie, Hepatologie et Nutrition, Lyon
CHU de Marseille, Hôpital de la Timone, Marseille
Medizinische Hochschule Hannover, Hanover
Hospital Papa Giovanni XXIII / Unità di Pediatria, Bergamo
Ospedale Pediatrico Bambino Gesu, Roma
Hotel Dieu de France, Beirut
Consultario de Joshue David Covarrubias Esquer, Zapopan
Instytut Pomnik Centrum Zdrowia Dziecka, Warsaw
KK Women's and Children's Hospital, Singapore
Koc University Hospital, Istanbul
Birmingham Children's Hospital, Birmingham
King's College Hospital NHS, London
Lead Sponsor
Mirum Pharmaceuticals, Inc.
INDUSTRY