90
Participants
Start Date
March 21, 2019
Primary Completion Date
July 3, 2024
Study Completion Date
July 3, 2024
AG-348
Participants will receive 5, 20, or 50 mg twice a day for up to 192 weeks (not including dose taper) unless the dose is modified for reasons related to safety.
Centre Hospitalier Universitaire Vaudois (CHUV), Vaud (Lausanne)
Herlev University Hospital, Herlev
Toho University Omori Medical Center, Tokyo
Charite - UB - CVK - Medizinische Klinik, Berlin
Faculty of Medicine Siriraj Hospital, Bangkok
Hospital La Timone, Marseille
Ospedale Galliera, Genova
Osp Maggiore Policlinico Milano, Milan
Duke University Medical Center, Durham
Hospital Universitario La Paz, Madrid
Htal Clínico Universitario Virgen de la Arrixaca., Murcia
Emory-Children's Center, Atlanta
Institut Universitaire du Cancer de Toulouse - Oncopole, Toulouse
CHU Hopitaux de Bordeaux - Hôpital Saint-André, Bordeaux
Cincinnati Children's Hospital Medical Center, Cincinnati
Indiana Hemophilia & Thrombosis Center Inc., Indianapolis
Wayne State University School of Medicine, Detroit
Houston Methodist Research Institute, Houston
"Università della Campania Luigi Vanvitelli", Napoli
University of Utah, Salt Lake City
Phoenix Children's Hospital, Phoenix
CHU Hôpital Henri Mondor, Créteil
UCSF Benioff Children's Hospital, Oakland, Oakland
Universitätsklinik Würzburg, Würzburg
Seattle Cancer Care Alliance, Seattle
Massachusetts General Hospital, Boston
Boston Children's Hospital, Boston
UNICAMP - Hemocentro, São Paulo
McMaster University, Hamilton
St James's Hospital, Dublin
AORN Cardarelli, Napoli
Mie University Hospital, Tsu
Tohoku University Hospital, Sendai
Kyoto Katsura Hospital, Kyoto
Kansai Medical University, Dep. of Pediatrics, Hirakata Hospital, Osaka
Van Creveldkliniek, Utrecht
Yeungnam University Hospital, Daegu
Hospital. U. Vall d'Hebron, Barcelona
Hacettepe University Faculty of Medicine, Ankara
Addenbrooke's Hospital, Cambridge
Imperial College Healthcare NHS Trust, London
University College London, London
Lead Sponsor
Agios Pharmaceuticals, Inc.
INDUSTRY