80
Participants
Start Date
August 9, 2018
Primary Completion Date
October 9, 2020
Study Completion Date
October 9, 2020
Placebo
Placebo matching AG-348 tablets, administered to maintain the blind.
AG-348
AG-348 tablets.
Centre Hospitalier Universitaire Vaudois (CHUV), Lausanne
University of Copenhagen, Herlev Hospital, Herlev
Universitair Medisch Centrum Utrecht, Utrecht
Department of Paediatrics and Thalassaemia Center, Faculty of Medicine Siriraj, Bangkok
Hôpital de la Timone, Marseille
Ospedale Galliera, Genova
Fondazione IRCCS Ca' Granda, Ospedale Maggiore Policlinico, Milan
Duke University, Durham
East Carolina University, Greenville
Hospital Universitario La Paz, Madrid
Hospital Clinico Universitario Virgen de la Arricaxa, El Palmar
Emory University, Atlanta
Yeungnam University Hospital, Daegu 705-703
Cincinnati Children's Hospital Medical Center, Cincinnati
Indiana Hemophilia and Thrombosis Center, Indianapolis
Wayne State University School of Medicine, Children's Hospital of Michigan, Detroit
University of Arkansas for Medical Sciences, Little Rock
Houston Methodist Research Institute, Houston
CHU Amiens Picardie, Amiens
"AOU Policlinico, Università della Campania Luigi Vanvitelli", Napoli
Primary Children's Hospital Univ. of Utah, Salt Lake City
Hôpital Henri-Mondor, Créteil
Addenbrooke's Hospital, Cambridge
Universitätsklinikum Würzburg, Würzburg
Seattle Cancer Care Alliance, Seattle
Massachusetts General Hospital, Boston
The Children's Hospital Corporation d/b/a Boston's Children Hospital, Boston
Hospital Central da Faculdade de Medicina USP Cidade Universitaria, São Paulo
Institute of Hematology and Blood Transfusion, Prague
Hopital Saint-Andre, Bordeaux
Institut Claudius Regaud, Toulouse
Charite University Medicine, Berlin
Tohoku University Hospital, Sendai
Kyoto Katsura Hospital, Kyoto
Agios Investigative Site, Mie
Kansai Medical University, Department of Pediatrics, Hirakata Hospital, Osaka
Toho University Omori Medical Center, Tokyo
Hacettepe University, Ankara
McMaster University - Health Sciences Centre, Hamilton
Toronto General Hospital, University Health Network, Toronto
Osaka City General Hospital, Osaka
Hospital U. Vall d'Hebron Servicio de Hematología Clínica, Barcelona
The Royal Liverpool and Broadgreen University, Liverpool
Imperial College Healthcare NHS Trust, Hammersmith Hospital, London
University College London, London
Manchester Royal Infirmary, Manchester
Lead Sponsor
Agios Pharmaceuticals, Inc.
INDUSTRY