Pyruvate Kinase Deficiency Global Longitudinal Registry

Active, not recruitingOBSERVATIONAL
Enrollment

500

Participants

Timeline

Start Date

April 23, 2018

Primary Completion Date

May 31, 2027

Study Completion Date

May 31, 2027

Conditions
Pyruvate Kinase Deficiency
Trial Locations (52)

144

Ospedale S Eugenio, Roma

2730

Copenhagen University Hospital, Herlev

8041

Hospital de La Santa Creu i Sant Pau, Barcelona

13353

Charite - Universitatsmedizin Berlin, Berlin

16128

E O Ospedali Galliera, Genoa

19104

Children's Hospital of Philadelphia, Philadelphia

20122

Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico, Milan

27710

Duke University Medical Center, Durham

28009

Hospital Infantil Universitario Nino Jesus, Madrid

28046

Hospital Universitario La Paz, Madrid

30342

Children's Healthcare of Atlanta, Atlanta

33617

Evangelisches Krankenhaus Bielefeld gGmbH, Bielefeld

38105

St Jude Children's Research Hospital, Memphis

43500

Hospital de Tortosa Verge de la Cinta, Tortosa

48201

Children's Hospital of Michigan, Detroit

65125

Presidio Ospedaliero di Pescara, Pescara

69120

Universitatsklinikum Heidelberg, Heidelberg

72202

Arkansas Children's Hospital, Little Rock

72205

University of Arkansas for Medical Sciences, Little Rock

75743

Hopital Necker, Paris

81377

Kinder- und Jugendarztpraxis, Munich

84113

Primary Children's Hospital, Salt Lake City

85016

Phoenix Childrens Hospital, Phoenix

92868

Children's Hospital of Orange County, Orange

94304

Stanford University Medical Center, Palo Alto

97080

Universitatsklinikum Wurzburg, Würzburg

02114

Massachusetts General Hospital, Boston

02115

Boston Children's Hospital, Boston

01655-0002

UMass Memorial Medical Center, Worcester

05401

University of Vermont Medical Center, Burlington

L8N 4A6

Saint Josephs Healthcare System, Hamilton

M5G 2C4

Toronto General Hospital, Toronto

H3T 1C5

St. Justine Hospital, Montreal

779 00

Fakultni nemocnice Olomouc, Olomouc

128 20

Ustav hematologie a krevni transfuze, Prague

150 06

Fakultni nemocnice v Motole, Prague

D08 NHY1

St James's Hospital, Dublin

Unknown

AOU dell'Universita degli Studi della Campania Luigi Vanvitelli, Napoli

The Catholic University of Korea, Seoul St. Mary's Hospital, Seoul

Siriraj Hospital Mahidol University, Bangkok

Hacettepe University Medical Faculty, Ankara

3508 GA

Universitair Medisch Centrum Utrecht, Utrecht

3041-853

Centro Hospitalar E Universitario de Coimbra EPE, Coimbra

1169-045

Centro Hospitalar Lisboa Central- Hospital Dona Estefania, Lisbon

4200-072

Centro Hospitalar de Vila Nova de Gaia / Espinho E.P.E, Porto

08916

Hospital Universitario Germans Trias i Pujol, Badalona

08950

Hospital Sant Joan de Deu - PIN, Esplugues de Llobregat

08035

Hospital Universitario Vall d'Hebron - PPDS, Barcelona

CH 1011

Centre Hospitalier Universitaire Vaudois, Lausanne

W12 0HS

Hammersmith Hospital, London

SE5 9RS

Kings College Hospital, London

NE1 4LP

The Newcastle Upon Tyne Hospitals NHS Foundation Trust, Newcastle upon Tyne

Sponsors
All Listed Sponsors
lead

Agios Pharmaceuticals, Inc.

INDUSTRY