500
Participants
Start Date
April 23, 2018
Primary Completion Date
May 31, 2027
Study Completion Date
May 31, 2027
Ospedale S Eugenio, Roma
Copenhagen University Hospital, Herlev
Hospital de La Santa Creu i Sant Pau, Barcelona
Charite - Universitatsmedizin Berlin, Berlin
E O Ospedali Galliera, Genoa
Children's Hospital of Philadelphia, Philadelphia
Fondazione IRCCS Ca Granda Ospedale Maggiore Policlinico, Milan
Duke University Medical Center, Durham
Hospital Infantil Universitario Nino Jesus, Madrid
Hospital Universitario La Paz, Madrid
Children's Healthcare of Atlanta, Atlanta
Evangelisches Krankenhaus Bielefeld gGmbH, Bielefeld
St Jude Children's Research Hospital, Memphis
Hospital de Tortosa Verge de la Cinta, Tortosa
Children's Hospital of Michigan, Detroit
Presidio Ospedaliero di Pescara, Pescara
Universitatsklinikum Heidelberg, Heidelberg
Arkansas Children's Hospital, Little Rock
University of Arkansas for Medical Sciences, Little Rock
Hopital Necker, Paris
Kinder- und Jugendarztpraxis, Munich
Primary Children's Hospital, Salt Lake City
Phoenix Childrens Hospital, Phoenix
Children's Hospital of Orange County, Orange
Stanford University Medical Center, Palo Alto
Universitatsklinikum Wurzburg, Würzburg
Massachusetts General Hospital, Boston
Boston Children's Hospital, Boston
UMass Memorial Medical Center, Worcester
University of Vermont Medical Center, Burlington
Saint Josephs Healthcare System, Hamilton
Toronto General Hospital, Toronto
St. Justine Hospital, Montreal
Fakultni nemocnice Olomouc, Olomouc
Ustav hematologie a krevni transfuze, Prague
Fakultni nemocnice v Motole, Prague
St James's Hospital, Dublin
AOU dell'Universita degli Studi della Campania Luigi Vanvitelli, Napoli
The Catholic University of Korea, Seoul St. Mary's Hospital, Seoul
Siriraj Hospital Mahidol University, Bangkok
Hacettepe University Medical Faculty, Ankara
Universitair Medisch Centrum Utrecht, Utrecht
Centro Hospitalar E Universitario de Coimbra EPE, Coimbra
Centro Hospitalar Lisboa Central- Hospital Dona Estefania, Lisbon
Centro Hospitalar de Vila Nova de Gaia / Espinho E.P.E, Porto
Hospital Universitario Germans Trias i Pujol, Badalona
Hospital Sant Joan de Deu - PIN, Esplugues de Llobregat
Hospital Universitario Vall d'Hebron - PPDS, Barcelona
Centre Hospitalier Universitaire Vaudois, Lausanne
Hammersmith Hospital, London
Kings College Hospital, London
The Newcastle Upon Tyne Hospitals NHS Foundation Trust, Newcastle upon Tyne
Lead Sponsor
Agios Pharmaceuticals, Inc.
INDUSTRY