A Clinical Trial of Retinal Gene Therapy for X-linked Retinitis Pigmentosa Using BIIB112

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

50

Participants

Timeline

Start Date

March 8, 2017

Primary Completion Date

November 18, 2020

Study Completion Date

November 18, 2020

Conditions
X-Linked Retinitis Pigmentosa
Interventions
BIOLOGICAL

BIIB112

Administered as specified in the treatment arm.

Trial Locations (8)

19104

Research Site, Philadelphia

32607

Research Site, Gainesville

33136

Research Site, Miami

75231

Research Site, Dallas

97239

Research Site, Portland

Unknown

Research Site, Manchester

Research Site, Oxford

Research Site, Southampton

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Biogen

INDUSTRY