292
Participants
Start Date
November 4, 2015
Primary Completion Date
August 21, 2023
Study Completion Date
August 21, 2023
nusinersen
Administered by intrathecal (IT) injection
Universitair Kinderziekenhuis Koningin Fabiola, Brussels
Sydney Children's Hospital Clinical Research Centre, Sydney
Royal Children's Hospital, Parkville
Seoul National University Hospital, Seoul
Uníversity of Hacettepe, Ankara
Columbia University Medical Center, New York
Istituto Giannina Gaslini, Centro Traslazionale di Miologia, Genova
Children's Hospital of Philadelphia, Philadelphia
The Johns Hopkins Hospital, Baltimore
Duke University School of Medicine, Durham
Duke University School of Medicine, Miyagi
Hospital Universitario La Paz, Madrid
Nemours Children's Clinic, Orlando
Marmara University Pendik Training and Research Hospital, Istanbul
Universitatsklinikum Essen, Essen
Gillette Children's Specialty Healthcare, Saint Paul
Ann & Robert H. Lurie Children's Hospital of Chicago, New York
Washington University School of Medicine, St Louis
Armand Trousseau Hospital, I-Motion, Paris
Children's Medical Center, Dallas
Universitaetsklinikum Freiburg, Freiburg im Breisgau
Children's Hospital Colorado, Aurora
LMU-Campus Innenstadt, Munich
University of Utah, Obu, Aichi
Stanford University School of Medicine, Palo Alto
Oregon Health Sciences University, Durham
Seattle Children's Hospital, Seattle
Department of Neuroscience, Università di Messina, AOU Polic, Messina
The University of Hong Kong, Hong Kong
David Geffen School of Medicine at UCLA, Los Angeles
Connecticut Children's Medical Center, Hartford
Boston Children's Hospital, Boston
BC Children's Hospital / UBC, Vancouver
Children's Health Research Institute, Brussel
McGill University Health Centre, Montreal
Pediatric Neurology Unit, Catholic University, Essen
Aichi Children's Health and Medical Center, Ōbu
Hyogo College of Medicine, Nishinomiya
Tokyo Women's Medical University, Shinjuku-ku
Kumamoto University Hospital, Kumamoto
Miyagi Prefectural Children Hospital, Miyagi
University of Miyazaki Hospital, Miyazaki
Hospital Sant Joan de Deu, Barcelona
Hospital Universitario Vall de Hebron, Hebron
The Queen Silvia Children's Hospital, Gothenburg
MRC Centre for Neuromuscular Diseases at Newcastle, Newcastle
UCL Institute of Child Health, London
Lead Sponsor
Biogen
INDUSTRY