A Study for Participants With Spinal Muscular Atrophy (SMA) Who Previously Participated in Nusinersen (ISIS 396443) Investigational Studies

PHASE3CompletedINTERVENTIONAL
Enrollment

292

Participants

Timeline

Start Date

November 4, 2015

Primary Completion Date

August 21, 2023

Study Completion Date

August 21, 2023

Conditions
Spinal Muscular Atrophy
Interventions
DRUG

nusinersen

Administered by intrathecal (IT) injection

Trial Locations (47)

1020

Universitair Kinderziekenhuis Koningin Fabiola, Brussels

2031

Sydney Children's Hospital Clinical Research Centre, Sydney

3052

Royal Children's Hospital, Parkville

3080

Seoul National University Hospital, Seoul

6100

Uníversity of Hacettepe, Ankara

10032

Columbia University Medical Center, New York

16147

Istituto Giannina Gaslini, Centro Traslazionale di Miologia, Genova

19104

Children's Hospital of Philadelphia, Philadelphia

21287

The Johns Hopkins Hospital, Baltimore

27710

Duke University School of Medicine, Durham

Duke University School of Medicine, Miyagi

28046

Hospital Universitario La Paz, Madrid

32827

Nemours Children's Clinic, Orlando

34662

Marmara University Pendik Training and Research Hospital, Istanbul

45147

Universitatsklinikum Essen, Essen

55101

Gillette Children's Specialty Healthcare, Saint Paul

60611

Ann & Robert H. Lurie Children's Hospital of Chicago, New York

63110

Washington University School of Medicine, St Louis

75012

Armand Trousseau Hospital, I-Motion, Paris

75235

Children's Medical Center, Dallas

79106

Universitaetsklinikum Freiburg, Freiburg im Breisgau

80045

Children's Hospital Colorado, Aurora

80337

LMU-Campus Innenstadt, Munich

84112

University of Utah, Obu, Aichi

94305

Stanford University School of Medicine, Palo Alto

97239

Oregon Health Sciences University, Durham

98105

Seattle Children's Hospital, Seattle

98125

Department of Neuroscience, Università di Messina, AOU Polic, Messina

999077

The University of Hong Kong, Hong Kong

90095-8344

David Geffen School of Medicine at UCLA, Los Angeles

06106

Connecticut Children's Medical Center, Hartford

02115

Boston Children's Hospital, Boston

V6H 3V4

BC Children's Hospital / UBC, Vancouver

N6A 5W9

Children's Health Research Institute, Brussel

H4A 3J1

McGill University Health Centre, Montreal

00168

Pediatric Neurology Unit, Catholic University, Essen

474-0038

Aichi Children's Health and Medical Center, Ōbu

663-8501

Hyogo College of Medicine, Nishinomiya

162-8666

Tokyo Women's Medical University, Shinjuku-ku

860-8556

Kumamoto University Hospital, Kumamoto

989-3126

Miyagi Prefectural Children Hospital, Miyagi

889-1692

University of Miyazaki Hospital, Miyazaki

08950

Hospital Sant Joan de Deu, Barcelona

08035

Hospital Universitario Vall de Hebron, Hebron

SE 416 86

The Queen Silvia Children's Hospital, Gothenburg

NE1 3BZ

MRC Centre for Neuromuscular Diseases at Newcastle, Newcastle

WC1N 1EH

UCL Institute of Child Health, London

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Biogen

INDUSTRY