NCT02520934View on ClinicalTrials.gov

Miglustat on Gaucher Disease Type IIIB

NAUnknownINTERVENTIONAL

Enrollment

19

Participants

Timeline

Start Date

July 31, 2015

Primary Completion Date

December 31, 2017

Study Completion Date

December 31, 2019

Conditions

Gaucher Disease

Interventions

DRUG

Miglustat

combine miglustat and ERT to see if neurologic manifestations can be improved

DRUG

ERT

enzyme replacement therapy

Trial Locations (1)

10041

National Taiwan University Hospital, Taipei

Sponsors

Collaborators (1)

All Listed Sponsors

collaborator

Actelion

INDUSTRY

lead

National Taiwan University Hospital

OTHER