Long Term Safety Study of Orfadin Treatment in HT-1 Patients in Standard Clinical Care

CompletedOBSERVATIONAL
Enrollment

315

Participants

Timeline

Start Date

September 30, 2013

Primary Completion Date

September 30, 2019

Study Completion Date

September 30, 2019

Conditions
Hereditary Tyrosinemia, Type I
Interventions
DRUG

Nitisinone

Nitisinone according to prescription

Trial Locations (77)

14186

Swedish Orphan Biovitrum Investigational Site, Stockholm

Unknown

Swedish Orphan Biovitrum Investigational Site, Innsbruck

Swedish Orphan Biovitrum Investigational Site, Vienna

Swedish Orphan Biovitrum Investigational Site, Antwerp

Swedish Orphan Biovitrum Investigational Site, Brussels

Swedish Orphan Biovitrum Investigational Site, Leuven

Swedish Orphan Biovitrum Investigational Site, Montegnée

Swedish Orphan Biovitrum Investigational Site, Woluwe-Saint-Lambert

Swedish Orphan Biovitrum Investigational Site, Prague

Swedish Orphan Biovitrum Investigational Site, Copenhagen

Swedish Orphan Biovitrum Investigational Site, Tampere

Swedish Orphan Biovitrum Investigational Site, Turku

Swedish Orphan Biovitrum Investigational Site, Angers

Swedish Oprhan Biovitrum Investigational Site, Lille

Swedish Orphan Biovitrum Investigational Site, Lyon

Swedish Orphan Biovitrum Investigational Site, Nantes

Swedish Oprhan Biovitrum Investigational Site, Paris

Swedish Orphan Biovitrum Investigational Site, Paris

Swedish Orphan Biovitrum Investigational Site, Talence

Swedish Orphan Biovitrum Investigational Site, Düsseldorf

Swedish Orphan Biovitrum Investigational Site, Erlangen

Swedish Orphan Biovitrum Investigational Site, Freiburg im Breisgau

Swedish Orphan Biovitrum Investigational Site, Hanover

Swedish Orphan Biovitrum Investigational Site, Heidelberg

Swedish Orphan Biovitrum Investigational Site, Leipzig

Swedish Orphan Biovitrum Investigational Site, Magdeburg

Swedish Orphan Biovitrum Investigational Site, München

Swedish Orphan Biovitrum Investigational Site, Reutlingen

Swedish Orphan Biovitrum Investigational Site, Budapest

Swedish Oprhan Biovitrum Investigational Site, Szeged

Swedish Orphan Biovitrum Investigational Site, Dublin

Swedish Orphan Biovitrum Investigational Site, Bari

Swedish Orphan Biovitrum Investigational Site, Catania

Swedish Orphan Biovitrum Investigational Site, Florence

Swedish Orphan Biovitrum Investigational Site, Milan

Swedish Orphan Biovitrum Investigational Site, Monza

Swedish Orphan Biovitrum Investigational Site, Napoli

Swedish Orphan Biovitrum Investigational Site, Padua

Swedish Orphan Biovitrum Investigational Site, Roma

Swedish Orphan Biovitrum Investigational Site, Saliceto

Swedish Orphan Biovitrum Investigational Site, Torino

Swedish Oprhan Biovitrum Investigational Site, Amsterdam

Swedish Orphan Biovitrum Investigational Site, Utrecht

Swedish Orphan Biovitrum Investigational Site, Fredrikstad

Swedish Orphan Biovitrum Investigational Site, Levanger

Swedish Oprhan Biovitrum Investigational Site, Oslo

Swedish Orphan Biovitrum Investigational Site, Oslo

Swedish Orphan Biovitrum Investigational Site, Tromsø

Swedish Oprhan Biovitrum Investigational Site, Warsaw

Swedish Orphan Biovitrum Investigational Site, Warsaw

Swedish Orphan Biovitrum Investigational Site, Coimbra

Swedish Orphan Biovitrum Investigational Site, Albacete

Swedish Orphan Biovitrum Investigational Site, Almería

Swedish Orphan Biovitrum Investigational Site, Badalona

Swedish Orphan Biovitrum Investigational Site, Barakaldo

Swedish Orphan Biovitrum Investigational Site, Barcelona

Swedish Orphan Biovitrum Investigational Site, Las Palmas de Gran Canaria

Swedish Oprhan Biovitrum Investigational Site, Madrid

Swedish Orphan Biovitrum Investigational Site, Madrid

Swedish Orphan Biovitrum Investigational Site, Málaga

Swedish Orphan Biovitrum Investigational Site, Mérida

Swedish Orphan Biovitrum Investigational Site, Murcia

Swedish Orphan Biovitrum Investigational Site, Pamplona

Swedish Orphan Biovitrum Investigational Site, Santiago

Swedish Orphan Biovitrum Investigational Site, Seville

Swedish Orphan Biovitrum Investigational Site, Valencia

Swedish Orphan Biovitrum Investigational Site, Gothenburg

Swedish Orphan Biovitrum Investigational Site, Stockholm

Swedish Orphan Biovitrum Investigational Site, Umeå

Swedish Orphan Biovitrum Investigational Site, Uppsala

Swedish Oprhan Biovitrum Investigational Site, Birmingham

Swedish Orphan Biovitrum Investigational Site, Bradford

Swedish Oprhan Biovitrum Investigational Site, London

Swedish Orphan Biovitrum Investigational Site, London

Swedish Oprhan Biovitrum Investigational Site, Manchester

Swedish Orphan Biovitrum Investigational Site, Manchester

Swedish Orphan Biovitrum Investigational Site, Sheffield

Sponsors
All Listed Sponsors
lead

Swedish Orphan Biovitrum

INDUSTRY