126
Participants
Start Date
November 24, 2014
Primary Completion Date
February 20, 2017
Study Completion Date
February 20, 2017
Nusinersen
Administered by intrathecal (IT) lumbar puncture (LP) injection
Sham procedure
Small needle prick on the lower back at the location where the IT injection is normally made
Columbia University Medical Center, New York
Children's Hospital of Philadelphia - Neurology, Philadelphia
Nemours Children's Hospital, Orlando
Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago
Washington University School of Medicine, St Louis
Children's Medical Center, Dallas
Children's Hospital Colorado, Aurora
UCLA Clinical and Translational Research Center, Los Angeles
Lucile Packard Children's Hospital at Stanford, Palo Alto
Oregon Health & Science University, Portland
Boston Children's Hospital, Boston
Children's Hospital - London Health Sciences Centre, London
McGill University Health Centre-Glen Site-CIM, Montreal
Armand Trousseau Hospital, I-Motion, Clinical Trials Platform, Paris
Universitatsklinikum Essen, Essen
University Hospital Freiberg, Center for Paediatrics and Adolescent Medicine, Department of Neuropaediatrics and Muscular Disease, Freiburg im Breisgau
The University of Hong Kong, Queen Mary Hospital, Department of Paediatrics and Adolescent Medicine, Hong Kong
AOU Policlinico G. Martino Dipartimento di Neuroscienze e Centro Clinico Nemo Sud, Messina
Fondazione Policlinico Universitario Agostino Gemelli-Universita Cattolica de Sacro Cuore-UOC Neuropsichiatre Infantile, Rome
Hyogo College of Medicine, Nishinomya-shi
Tokyo Women's Medical University, Shinjuku-ku
Seoul National University Children's Hospital, Seoul
Hospital Sant Joan de Deu, Barcelona
University of Gothenburg, The Queen Silvia Children's Hospital, Gothenburg
Lead Sponsor
Biogen
INDUSTRY