254
Participants
Start Date
December 31, 2013
Primary Completion Date
December 31, 2019
Study Completion Date
May 31, 2020
Weill Cornell Medical College, New York
Central Pennsylvania Clinic, Strasburg
Children's Hospital of Philadelphia, Philadelphia
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan
Duke University Medical Center, Durham
Children's Hospital of Atlanta, Atlanta
Klinikum Kassel, Kassel
St. Jude Children's Research Hospital, Memphis
University of Mississippi Medical Center, Jackson
Nationwide Children's Hospital, Columbus
DDC Clinic for Special Needs Children, Middlefield
Wayne State University School of Medicine, Detroit
Lurie Children's Hospital, Chicago
Children's Mercy Hospitals & Clinics, Kansas City
UniversitätsKlinikum Heidelberg, Zentrum für Kinder- und Jugendmedizin Klinik Kinderheilkunde III, Heidelberg
Baylor College of Medicine, Houston
University of Freiburg, Freiburg im Breisgau
Klinikum der Universität München, Center for Pediatric Hematology/Hemostaseology, Munich
University of Utah, Salt Lake City
Phoenix Children's Hospital, Phoenix
Stanford University, Palo Alto
Boston Children's Hospital, Boston
University of Massachusetts Medical Center, Worcester
University of Vermont College of Medicine & University of Vermont Medical Center, Burlington
McMaster University, Hamilton
University Health Network, Toronto
CHU Sainte-Justine, Montreal
Fakultni Nemocnice Olomouc, Olomouc
Charite Berlin, Berlin
UMC Utrecht, Utrecht
Collaborators (1)
Agios Pharmaceuticals, Inc.
INDUSTRY
Boston Children's Hospital
OTHER