Pyruvate Kinase Deficiency Natural History Study

CompletedOBSERVATIONAL
Enrollment

254

Participants

Timeline

Start Date

December 31, 2013

Primary Completion Date

December 31, 2019

Study Completion Date

May 31, 2020

Conditions
Pyruvate Kinase DeficiencyCongenital Non-Spherocytic Hemolytic Anemia
Trial Locations (30)

10065

Weill Cornell Medical College, New York

17579

Central Pennsylvania Clinic, Strasburg

19104

Children's Hospital of Philadelphia, Philadelphia

20122

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan

27710

Duke University Medical Center, Durham

30342

Children's Hospital of Atlanta, Atlanta

34125

Klinikum Kassel, Kassel

38105

St. Jude Children's Research Hospital, Memphis

39216

University of Mississippi Medical Center, Jackson

43205

Nationwide Children's Hospital, Columbus

44062

DDC Clinic for Special Needs Children, Middlefield

48201

Wayne State University School of Medicine, Detroit

60611

Lurie Children's Hospital, Chicago

64108

Children's Mercy Hospitals & Clinics, Kansas City

69120

UniversitätsKlinikum Heidelberg, Zentrum für Kinder- und Jugendmedizin Klinik Kinderheilkunde III, Heidelberg

77030

Baylor College of Medicine, Houston

79106

University of Freiburg, Freiburg im Breisgau

80337

Klinikum der Universität München, Center for Pediatric Hematology/Hemostaseology, Munich

84108

University of Utah, Salt Lake City

85006

Phoenix Children's Hospital, Phoenix

94305

Stanford University, Palo Alto

02115

Boston Children's Hospital, Boston

01605

University of Massachusetts Medical Center, Worcester

05405

University of Vermont College of Medicine & University of Vermont Medical Center, Burlington

L8N 3Z5

McMaster University, Hamilton

M5G 2C4

University Health Network, Toronto

H3T 1C5

CHU Sainte-Justine, Montreal

Unknown

Fakultni Nemocnice Olomouc, Olomouc

Charite Berlin, Berlin

3508GA

UMC Utrecht, Utrecht

Sponsors
All Listed Sponsors
collaborator

Agios Pharmaceuticals, Inc.

INDUSTRY

lead

Boston Children's Hospital

OTHER