Taste and Palatability of Orfadin Suspension

PHASE1CompletedINTERVENTIONAL
Enrollment

18

Participants

Timeline

Start Date

October 31, 2012

Primary Completion Date

March 31, 2013

Study Completion Date

March 31, 2013

Conditions
Hereditary Tyrosinemia, Type I
Interventions
DRUG

Nitisinone

Oral suspension

Trial Locations (7)

Unknown

Hopital Necker, Paris

Universitätsklinikum Düsseldorf, Düsseldorf

Universitätsklinikum Heidelberg, Heidelberg

Klinikum der Universität München, München

Birmingham Children's Hospital, Birmingham

Evelina Children's Hospital, St Thomas' Hospital, London

St Mary's Hospital, Manchester

Sponsors
All Listed Sponsors
lead

Swedish Orphan Biovitrum

INDUSTRY