About
Small Molecules for Rare Diseases
Areas of Focus
Categories
Small Molecule Pharmaceutical
Clinical Trials (5)
View allTotal Trials
5
As Lead Sponsor
5
As Collaborator
0
Total Enrollment
237
By Phase
PHASE3: 1PHASE2: 2PHASE2/PHASE3: 1
By Status
RECRUITING: 2COMPLETED: 2UNKNOWN: 1
Clinical Trials Pipeline5 trials
Early Phase 1
Phase 1
Phase 2
Phase 3
Phase 4
Phase 1/2
Phase 2/3
N/A
2016
2017
2018
2019
2020
2021
2022
2023
2024
2025
2026
2027
2028
Today
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Recent Trials
NCT06178120Lead Sponsor
Disease Progression in Women With X-linked Adrenoleukodystrophy
N/ARecruiting
40 participants
Started: Jan 2, 2024 · Completed: Jun 30, 2027
NCT05819866Lead Sponsor
A Clinical Study to Assess the Efficacy and Safety of Leriglitazone in Adult Male Subjects With Cerebral Adrenoleukodystrophy
PHASE3Recruiting
40 participants
Started: Jul 12, 2023 · Completed: May 31, 2027
NCT04528706Lead Sponsor
A Clinical Study in Male Pediatric Patients With Cerebral X-linked Adrenoleukodystrophy (Cald) to Assess the Effects of MIN-102 Treatment on Disease Progression Prior to Human Stem Cell Transplant (HSCT)
PHASE2Unknown
13 participants
Started: Sep 13, 2019 · Completed: Dec 31, 2023
NCT03917225Lead Sponsor
A Clinical Study to Evaluate the Effect of MIN-102 on the Progression of Friedreich's Ataxia in Male and Female Patients
PHASE2Completed
39 participants
Started: Mar 26, 2019 · Completed: Sep 14, 2020
NCT03231878Lead Sponsor
A Clinical Study to Evaluate the Efficacy and Safety of MIN-102 (IMP) in Male AMN Patients.
PHASE2/PHASE3Completed
105 participants
Started: Dec 8, 2017 · Completed: Mar 6, 2025
Locations (1)
Headquarters
Barcelona, Spain
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